Our journey to successful gene therapy for hemophilia B.

about

Progress and challenges in viral vector manufacturing Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs.Gene Therapy for Hemophilia.

P2860

Q36713761-FB97394F-EA69-47EA-A516-6AF996D15B88 Q40318313-2908B2C4-3269-4455-B8A6-B0D3ABF35DA9 Q51057724-20A8457A-6BB1-4C35-904E-0639814CB7D4

P2860

Our journey to successful gene therapy for hemophilia B.

Item

http://www.wikidata.org/entity/Q38562869

description

2014 nî lūn-bûn

@nan

2014年の論文

@ja

2014年論文

@yue

2014年論文

@zh-hant

2014年論文

@zh-hk

2014年論文

@zh-mo

2014年論文

@zh-tw

2014年论文

@wuu

2014年论文

@zh

2014年论文

@zh-cn

name

Our journey to successful gene therapy for hemophilia B.

@en

type

Item

label

Our journey to successful gene therapy for hemophilia B.

@en

prefLabel

Our journey to successful gene therapy for hemophilia B.

@en

P1476

Our journey to successful gene therapy for hemophilia B.

@en

P2093

Amit C Nathwani

http://www.w3.org/2001/XMLSchema#string

Andrew M Davidoff

http://www.w3.org/2001/XMLSchema#string

Arthur W Nienhuis

http://www.w3.org/2001/XMLSchema#string

P2860

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

Design and packaging of adeno-associated virus gene targeting vectors

Seroepidemiological and ecological studies of the adenovirus-associated satellite viruses

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

Rapid and highly efficient transduction by double-stranded adeno-associated virus vectors in vitro and in vivo.

Update on the use of nonhuman primate models for preclinical testing of gene therapy approaches targeting hematopoietic cells.

Virus-mediated transduction of murine retina with adeno-associated virus: effects of viral capsid and genome size.

Good manufacturing practice production of self-complementary serotype 8 adeno-associated viral vector for a hemophilia B clinical trial

Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.

P304

923-926

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.1089/HUM.2014.2540

http://www.w3.org/2001/XMLSchema#string

P433

http://www.w3.org/2001/XMLSchema#string

P478

http://www.w3.org/2001/XMLSchema#string

P577

2014-11-01T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P698

25397929

http://www.w3.org/2001/XMLSchema#string

P921

hemophilia

gene therapy

hemophilia B

P932

4236090

http://www.w3.org/2001/XMLSchema#string

Our journey to successful gene therapy for hemophilia B.

about

P2860

P2860

Our journey to successful gene therapy for hemophilia B.

description

name

type

label

prefLabel

P1433

P1476

P2093

P2860

P304

P31

P356

P433

P478

P577

P698

P921

P932

P356

P1433

P1476

P2093

P2860

P304

P31

P356

P433

P478

P577

P698

P921

P932