High-dose enzyme replacement therapy in murine Hurler syndrome
about
Effects of enzyme replacement therapy started late in a murine model of mucopolysaccharidosis type ICNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)Transcranial pulsed ultrasound facilitates brain uptake of laronidase in enzyme replacement therapy for Mucopolysaccharidosis type I diseaseAssessment of dysmyelination with RAFFn MRI: application to murine MPS I.Enzyme replacement therapy and beyond-in memoriam Roscoe O. Brady, M.D. (1923-2016).Lysosomal storage disease: gene therapy on both sides of the blood-brain barrier.Molecular Genetics and Metabolism Report Long-term follow-up of post hematopoietic stem cell transplantation for Hurler syndrome: clinical, biochemical, and pathological improvements.Neurocognition across the spectrum of mucopolysaccharidosis type I: Age, severity, and treatment.Effect of systemic high dose enzyme replacement therapy on the improvement of CNS defects in a mouse model of mucopolysaccharidosis type IIChronic enzyme replacement therapy ameliorates neuropathology in alpha-mannosidosis miceProteomic analysis of mucopolysaccharidosis I mouse brain with two-dimensional polyacrylamide gel electrophoresis.Elements of lentiviral vector design toward gene therapy for treating mucopolysaccharidosis I.RTB Lectin: a novel receptor-independent delivery system for lysosomal enzyme replacement therapiesLong-term cognitive and somatic outcomes of enzyme replacement therapy in untransplanted Hurler syndrome.RTB lectin-mediated delivery of lysosomal α-l-iduronidase mitigates disease manifestations systemically including the central nervous system.Long-term outcomes of systemic therapies for Hurler syndrome: an international multicenter comparison.Getting the Most: Enhancing Efficacy by Promoting Erythropoiesis and Thrombopoiesis after Gene Therapy in Mice with Hurler Syndrome
P2860
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P2860
High-dose enzyme replacement therapy in murine Hurler syndrome
description
2013 nî lūn-bûn
@nan
2013年の論文
@ja
2013年学术文章
@wuu
2013年学术文章
@zh-cn
2013年学术文章
@zh-hans
2013年学术文章
@zh-my
2013年学术文章
@zh-sg
2013年學術文章
@yue
2013年學術文章
@zh
2013年學術文章
@zh-hant
name
High-dose enzyme replacement therapy in murine Hurler syndrome
@en
High-dose enzyme replacement therapy in murine Hurler syndrome.
@nl
type
label
High-dose enzyme replacement therapy in murine Hurler syndrome
@en
High-dose enzyme replacement therapy in murine Hurler syndrome.
@nl
prefLabel
High-dose enzyme replacement therapy in murine Hurler syndrome
@en
High-dose enzyme replacement therapy in murine Hurler syndrome.
@nl
P2093
P2860
P1476
High-dose enzyme replacement therapy in murine Hurler syndrome
@en
P2093
Brenda L Koniar
Chester B Whitley
Roland Gunther
Tyler Herzog
P2860
P304
P356
10.1016/J.YMGME.2013.09.008
P577
2013-09-19T00:00:00Z