Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
about
Aspartylglycosaminuria: a reviewReplacing the enzyme alpha-L-iduronidase at birth ameliorates symptoms in the brain and periphery of dogs with mucopolysaccharidosis type I.Enhancement of drug delivery: enzyme-replacement therapy for murine Morquio A syndrome.Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII.New strategies for enzyme replacement therapy for lysosomal storage diseasesEnzyme therapy in mannose receptor-null mucopolysaccharidosis VII mice defines roles for the mannose 6-phosphate and mannose receptorsThe potential investment impact of improved access to accelerated approval on the development of treatments for low prevalence rare diseasesEpinephrine enhances lysosomal enzyme delivery across the blood brain barrier by up-regulation of the mannose 6-phosphate receptorEffect of systemic high dose enzyme replacement therapy on the improvement of CNS defects in a mouse model of mucopolysaccharidosis type IILong circulating enzyme replacement therapy rescues bone pathology in mucopolysaccharidosis VII murine model.Biochemical evidence for superior correction of neuronal storage by chemically modified enzyme in murine mucopolysaccharidosis VII.Chronic enzyme replacement therapy ameliorates neuropathology in alpha-mannosidosis miceChemically modified beta-glucuronidase crosses blood-brain barrier and clears neuronal storage in murine mucopolysaccharidosis VII.Pharmacologic manipulation of lysosomal enzyme transport across the blood-brain barrier.Current and emerging management options for patients with Morquio A syndromeLysosomal enzyme replacement therapies: Historical development, clinical outcomes, and future perspectives.High-dose enzyme replacement therapy in murine Hurler syndromeEnzyme replacement improves ataxic gait and central nervous system histopathology in a mouse model of metachromatic leukodystrophy.White Matter Microstructure and Subcortical Gray Matter Structure Volumes in Aspartylglucosaminuria; a 5-Year Follow-up Brain MRI Study of an Adolescent with Aspartylglucosaminuria and His Healthy Twin Brother.Transport of arylsulfatase A across the blood-brain barrier in vitro.Induction of tolerance to human arylsulfatase A in a mouse model of metachromatic leukodystrophy.
P2860
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P2860
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
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2000 nî lūn-bûn
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2000 թուականի Փետրուարին հրատարակուած գիտական յօդուած
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2000 թվականի փետրվարին հրատարակված գիտական հոդված
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2000年の論文
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2000年論文
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2000年論文
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Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
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Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@en
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
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label
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@ast
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@en
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@nl
prefLabel
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@ast
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@en
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@nl
P2093
P1433
P1476
Enzyme replacement therapy in a mouse model of aspartylglycosaminuria
@en
P2093
E Väänänen
N Heisterkamp
P Valtonen
V Kaartinen
P407
P577
2000-02-01T00:00:00Z