Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy.
about
Molecular and cell-based therapies for muscle degenerations: a road under constructionSplicing therapy for neuromuscular diseaseRescue of cardiomyopathy through U7snRNA-mediated exon skipping in Mybpc3-targeted knock-in miceRescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skippingState-of-the-art human gene therapy: part II. Gene therapy strategies and clinical applications.Clinical phenotypes as predictors of the outcome of skipping around DMD exon 45.Exon 32 Skipping of Dysferlin Rescues Membrane Repair in Patients' CellsCurrent Translational Research and Murine Models For Duchenne Muscular Dystrophy.Repair or replace? Exploiting novel gene and cell therapy strategies for muscular dystrophies.Viral Vector-Mediated Antisense Therapy for Genetic Diseases.Localizing the RPGR protein along the cilium: a new method to determine efficacies to treat RPGR mutations.Targeting Splicing in the Treatment of Human DiseaseAAV genome loss from dystrophic mouse muscles during AAV-U7 snRNA-mediated exon-skipping therapy.Therapeutic effects of exon skipping and losartan on skeletal muscle of mdx mice.Activating internal ribosome entry to treat Duchenne muscular dystrophy
P2860
Q24568176-FD976DDA-BEA9-474B-84E7-6610B84D1BECQ27009581-B35B4C58-9107-4E84-9102-E9BA7172B2D5Q28291547-7667A947-6DB3-490A-890C-02450B234B27Q30514014-A82E138F-4466-45C4-80C6-D7B502B59434Q34664690-78535382-4D0C-4C3E-8182-70E8B4A8AD93Q35224393-8461E105-4265-40F8-AC34-F343F60F7EBCQ37589627-22FF157F-AF3E-4864-B713-8AF736142125Q37610505-E6E8085C-178D-4CDC-8F16-74919BAEE678Q38079633-53DF7DDB-B4CF-4B28-BAC6-9030F47039F9Q38289261-39B3381C-7FE9-43F6-9E8A-A1A2FF4FE34EQ38915580-35E0A659-E814-40B3-A578-5A693DB10E81Q39154733-5A42110A-B3DD-45FD-80B2-516CA44CC72DQ39404658-246C6088-A41B-4133-B27B-A07EA2696788Q53263857-B8C1AD1C-586E-49D1-8026-1CABB019E8ECQ57394241-631D5B96-DF2D-4A87-90F7-0A8FAC41297F
P2860
Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy.
description
2012 nî lūn-bûn
@nan
2012年の論文
@ja
2012年学术文章
@wuu
2012年学术文章
@zh-cn
2012年学术文章
@zh-hans
2012年学术文章
@zh-my
2012年学术文章
@zh-sg
2012年學術文章
@yue
2012年學術文章
@zh
2012年學術文章
@zh-hant
name
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@en
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@nl
type
label
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@en
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@nl
prefLabel
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@en
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@nl
P2093
P2860
P356
P1433
P1476
Engineering multiple U7snRNA c ...... r Duchenne muscular dystrophy.
@en
P2093
Arran Babbs
Aurélie Goyenvalle
Jordan Wright
Kay E Davies
Luis Garcia
Vivienne Wilkins
P2860
P304
P356
10.1038/MT.2012.26
P577
2012-02-21T00:00:00Z