Double-target antisense U7 snRNAs promote efficient skipping of an aberrant exon in three human beta-thalassemic mutations - Wikidata - wikimedia - TriplyDB

Double-target antisense U7 snRNAs promote efficient skipping of an aberrant exon in three human beta-thalassemic mutations

Double-target antisense U7 snRNAs promote efficient skipping of an aberrant exon in three human beta-thalassemic mutations

http://www.wikidata.org/entity/Q28137724

about

Evolutionary conservation of the U7 small nuclear ribonucleoprotein in Drosophila melanogaster.Inhibition of HIV-1 multiplication by antisense U7 snRNAs and siRNAs targeting cyclophilin A Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapy Antisense-mediated exon skipping: a versatile tool with therapeutic and research applications Doxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettes Antisense properties of tricyclo-DNA Future alternative therapies for β-thalassemia.Producing recombinant adeno-associated virus in foster cells: overcoming production limitations using a baculovirus-insect cell expression strategy.Reduction of target gene expression by a modified U1 snRNA.Chimeric snRNA molecules carrying antisense sequences against the splice junctions of exon 51 of the dystrophin pre-mRNA induce exon skipping and restoration of a dystrophin synthesis in Delta 48-50 DMD cells Nonsense-associated alternative splicing of T-cell receptor beta genes: no evidence for frame dependence Repair of pre-mRNA splicing: prospects for a therapy for spinal muscular atrophy.Duchenne muscular dystrophy gene therapy in the canine model.Viral-mediated gene therapy for the muscular dystrophies: successes, limitations and recent advances MRI roadmap-guided transendocardial delivery of exon-skipping recombinant adeno-associated virus restores dystrophin expression in a canine model of Duchenne muscular dystrophy.Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy.Gene therapy in thalassemia and hemoglobinopathies.Missing links in cardiology: long non-coding RNAs enter the arena.Analysis of the functional consequences of targeted exon deletion in COL7A1 reveals prospects for dystrophic epidermolysis bullosa therapy.Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy.The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery.Double-target Antisense U1snRNAs Correct Mis-splicing Due to c.639+861C>T and c.639+919G>A GLA Deep Intronic Mutations.Gene therapy: the 'pro-sense' approach to Duchenne muscular dystrophy.

P2860

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P2860

Double-target antisense U7 snRNAs promote efficient skipping of an aberrant exon in three human beta-thalassemic mutations

http://www.wikidata.org/entity/Q28137724

description

1999 nî lūn-bûn

@nan

1999 թուականի Դեկտեմբերին հրատարակուած գիտական յօդուած

@hyw

1999 թվականի դեկտեմբերին հրատարակված գիտական հոդված

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1999年の論文

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1999年論文

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1999年論文

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1999年論文

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1999年論文

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1999年論文

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1999年论文

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name

Double-target antisense U7 snR ...... man beta-thalassemic mutations

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Double-target antisense U7 snR ...... man beta-thalassemic mutations

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Double-target antisense U7 snR ...... man beta-thalassemic mutations

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type

label

Double-target antisense U7 snR ...... man beta-thalassemic mutations

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Double-target antisense U7 snR ...... man beta-thalassemic mutations

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Double-target antisense U7 snR ...... man beta-thalassemic mutations

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prefLabel

Double-target antisense U7 snR ...... man beta-thalassemic mutations

@ast

Double-target antisense U7 snR ...... man beta-thalassemic mutations

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Double-target antisense U7 snR ...... man beta-thalassemic mutations

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Human Molecular Genetics

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Double-target antisense U7 snR ...... man beta-thalassemic mutations

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P2093

D Suter

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L Gorman

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R Kole

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R Tomasini

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scholarly article

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10.1093/HMG/8.13.2415

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13

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8

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