CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease.
about
Function and safety of lentivirus-mediated gene transfer for CSF2RA-deficiency.Evolving Gene Therapy in Primary Immunodeficiency.Xenogeneic chimera-Generated by blastocyst complementation-As a potential unlimited source of recipient-tailored organs.Recent advances in understanding and treating chronic granulomatous disease.CRISPR-Mediated Integration of Large Gene Cassettes Using AAV Donor Vectors.CRISPR-Mediated Knockout of Cybb in NSG Mice Establishes a Model of Chronic Granulomatous Disease for Human Stem-Cell Gene Therapy Transplants.Very Early-Onset Inflammatory Manifestations of X-Linked Chronic Granulomatous Disease.Multiplexed genetic engineering of human hematopoietic stem and progenitor cells using CRISPR/Cas9 and AAV6.The changing landscape of gene editing in hematopoietic stem cells: a step towards Cas9 clinical translation.Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned.A Review of Chronic Granulomatous Disease.Efficacy of lentiviral mediated gene therapy in an Omenn syndrome Rag2 mouse model is not hindered by inflammation and immune dysregulation.Assembly of CRISPR ribonucleoproteins with biotinylated oligonucleotides via an RNA aptamer for precise gene editing.CRISPR/Cas9 Genome-Editing System in Human Stem Cells: Current Status and Future Prospects.Xenotransplantation: back to the future?Human genetic variation alters CRISPR-Cas9 on- and off-targeting specificity at therapeutically implicated loci.Genome-wide Mapping of Off-Target Events in Single-Stranded Oligodeoxynucleotide-Mediated Gene Repair Experiments.CRISPR/Cas9 genome editing in human hematopoietic stem cells.High Efficiency Gene Correction in Hematopoietic Cells by Donor-Template-Free CRISPR/Cas9 Genome Editing.Myeloid Conditioning with c-kit-Targeted CAR-T Cells Enables Donor Stem Cell Engraftment.CRISPR/Cas9: the Jedi against the dark empire of diseases.Chronic Granulomatous Disease: Epidemiology, Pathophysiology, and Genetic Basis of Disease.CRISPR/Cas9 System: A Bacterial Tailor for Genomic EngineeringChemical Tools for Targeted Amplification of Reactive Oxygen Species in Neutrophils
P2860
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P2860
CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease.
description
2017 nî lūn-bûn
@nan
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
2017年论文
@zh
2017年论文
@zh-cn
name
CRISPR-Cas9 gene repair of hem ...... chronic granulomatous disease.
@en
type
label
CRISPR-Cas9 gene repair of hem ...... chronic granulomatous disease.
@en
prefLabel
CRISPR-Cas9 gene repair of hem ...... chronic granulomatous disease.
@en
P2093
P2860
P1476
CRISPR-Cas9 gene repair of hem ...... chronic granulomatous disease
@en
P2093
Angelia Viley
Colin Sweeney
Cornell Allen
Douglas Kuhns
Jessica Chu
Lela Kardava
Linhong Li
Madhusudan V Peshwa
P2860
P356
10.1126/SCITRANSLMED.AAH3480
P407
P577
2017-01-01T00:00:00Z