Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
about
Moving towards effective therapeutic strategies for Neuronal Ceroid LipofuscinosisSialic acid deposition impairs the utility of AAV9, but not peptide-modified AAVs for brain gene therapy in a mouse model of lysosomal storage diseasePathogenesis and therapies for infantile neuronal ceroid lipofuscinosis (infantile CLN1 disease).Large-volume intrathecal enzyme delivery increases survival of a mouse model of late infantile neuronal ceroid lipofuscinosis.Liver production of sulfamidase reverses peripheral and ameliorates CNS pathology in mucopolysaccharidosis IIIA mice.Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophyBiochemical evidence for superior correction of neuronal storage by chemically modified enzyme in murine mucopolysaccharidosis VII.Considerations for the treatment of infantile neuronal ceroid lipofuscinosis (infantile Batten disease)Combination Therapies for Lysosomal Storage Diseases: A Complex Answer to a Simple Problem.
P2860
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P2860
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
description
2009 nî lūn-bûn
@nan
2009年の論文
@ja
2009年論文
@yue
2009年論文
@zh-hant
2009年論文
@zh-hk
2009年論文
@zh-mo
2009年論文
@zh-tw
2009年论文
@wuu
2009年论文
@zh
2009年论文
@zh-cn
name
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@en
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@nl
type
label
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@en
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@nl
prefLabel
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@en
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@nl
P2860
P1476
Promising CNS-directed enzyme replacement therapy for lysosomal storage diseases.
@en
P2093
Mark S Sands
Shannon L Macauley
P2860
P356
10.1016/J.EXPNEUROL.2009.03.040
P407
P577
2009-04-08T00:00:00Z