Half the dystrophin gene is apparently enough for a mild clinical course: confirmation of its potential use for gene therapy.
about
Induction of revertant fibres in the mdx mouse using antisense oligonucleotidesAdeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model.Jagged 1 Rescues the Duchenne Muscular Dystrophy Phenotype.Assessing pathogenicity for novel mutation/sequence variants: the value of healthy older individualsNeuromuscular disorders: genes, genetic counseling and therapeutic trialsStem cells from umbilical cord blood do have myogenic potential, with and without differentiation induction in vitroDystrophin mutations predict cellular susceptibility to oxidative stress.Dystrophin expression in host muscle following transplantation of muscle precursor cells modified with the phiC31 integrase.C-terminal truncated dystrophin identified in skeletal muscle of an asymptomatic boy with a novel nonsense mutation of the dystrophin gene.Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy
P2860
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P2860
Half the dystrophin gene is apparently enough for a mild clinical course: confirmation of its potential use for gene therapy.
description
1994 nî lūn-bûn
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1994年の論文
@ja
1994年学术文章
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1994年学术文章
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1994年学术文章
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1994年学术文章
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1994年学术文章
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1994年学术文章
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1994年學術文章
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1994年學術文章
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name
Half the dystrophin gene is ap ...... otential use for gene therapy.
@en
Half the dystrophin gene is ap ...... otential use for gene therapy.
@nl
type
label
Half the dystrophin gene is ap ...... otential use for gene therapy.
@en
Half the dystrophin gene is ap ...... otential use for gene therapy.
@nl
prefLabel
Half the dystrophin gene is ap ...... otential use for gene therapy.
@en
Half the dystrophin gene is ap ...... otential use for gene therapy.
@nl
P356
P1476
Half the dystrophin gene is ap ...... potential use for gene therapy
@en
P2093
M R Passos-Bueno
P304
P356
10.1093/HMG/3.6.919
P577
1994-06-01T00:00:00Z