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Q30493690-547CF8F2-FB2E-4AB8-B84C-AACFC94CB2B9
Q30493690-547CF8F2-FB2E-4AB8-B84C-AACFC94CB2B9
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Statement
http://www.wikidata.org/entity/statement/Q30493690-547CF8F2-FB2E-4AB8-B84C-AACFC94CB2B9
A self-inactivating gamma-retroviral vector reduces manifestations of mucopolysaccharidosis I in mice
P2860
Q30493690-547CF8F2-FB2E-4AB8-B84C-AACFC94CB2B9
BestRank
Statement
http://www.wikidata.org/entity/statement/Q30493690-547CF8F2-FB2E-4AB8-B84C-AACFC94CB2B9
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wasDerivedFrom
c4a149d94beae9f95f5e11e1e8000810a78fb2f6
P2860
AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice.