A self-inactivating gamma-retroviral vector reduces manifestations of mucopolysaccharidosis I in mice

A self-inactivating gamma-retroviral vector reduces manifestations of mucopolysaccharidosis I in mice

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http://www.wikidata.org/entity/Q30493690
Evidence of a progressive motor dysfunction in Mucopolysaccharidosis type I mice.Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI cats.Retroviral-vector-mediated gene therapy to mucopolysaccharidosis I mice improves sensorimotor impairments and other behavioral deficits.Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model.Upregulation of elastase activity in aorta in mucopolysaccharidosis I and VII dogs may be due to increased cytokine expression.Therapies of mucopolysaccharidosis IVA (Morquio A syndrome).Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type ILysosomal storage disease: gene therapy on both sides of the blood-brain barrier.Perinatal gene transfer to the liver.Pathogenesis of aortic dilatation in mucopolysaccharidosis VII mice may involve complement activation.Angiotensin receptor blockade mediated amelioration of mucopolysaccharidosis type I cardiac and craniofacial pathology.Standardization of α-L-iduronidase enzyme assay with Michaelis-Menten kinetics.Gene delivery strategies for the treatment of mucopolysaccharidoses.
P2860

A self-inactivating gamma-retroviral vector reduces manifestations of mucopolysaccharidosis I in mice

Item
http://www.wikidata.org/entity/Q30493690
description
2009 nî lūn-bûn
@nan
2009 թուականի Հոկտեմբերին հրատարակուած գիտական յօդուած
@hyw
2009 թվականի հոտեմբերին հրատարակված գիտական հոդված
@hy
2009年の論文
@ja
2009年論文
@yue
2009年論文
@zh-hant
2009年論文
@zh-hk
2009年論文
@zh-mo
2009年論文
@zh-tw
2009年论文
@wuu
name
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@ast
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@en
type
label
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@ast
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@en
prefLabel
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@ast
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@en
P1433
P1476
P2093
P2860
P304
P31
P356
P433
P478
P50
P577
P5875
P698
P932
P356
P1433
P1476
A self-inactivating gamma-retr ...... ucopolysaccharidosis I in mice
@en
P2093
P2860
P304
P31
P356
P433
P478
P50
P577
P5875
P698
P932