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Q33568024-02883F10-E1A8-4E9F-B659-F80FE56CDB1D
Q33568024-02883F10-E1A8-4E9F-B659-F80FE56CDB1D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33568024-02883F10-E1A8-4E9F-B659-F80FE56CDB1D
Evaluation of N-nonyl-deoxygalactonojirimycin as a pharmacological chaperone for human GM1 gangliosidosis leads to identification of a feline model suitable for testing enzyme enhancement therapy.
P2860
Q33568024-02883F10-E1A8-4E9F-B659-F80FE56CDB1D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33568024-02883F10-E1A8-4E9F-B659-F80FE56CDB1D
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type
BestRank
Statement
wasDerivedFrom
f7cb72fb6498cbdb2b05ef8ac38e7698348b3a41
P2860
DLHex-DGJ, a novel derivative of 1-deoxygalactonojirimycin with pharmacological chaperone activity in human G(M1)-gangliosidosis fibroblasts.