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Q33568024-46345A5A-0238-4AFC-92DB-22F914375626
Q33568024-46345A5A-0238-4AFC-92DB-22F914375626
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33568024-46345A5A-0238-4AFC-92DB-22F914375626
Evaluation of N-nonyl-deoxygalactonojirimycin as a pharmacological chaperone for human GM1 gangliosidosis leads to identification of a feline model suitable for testing enzyme enhancement therapy.
P2860
Q33568024-46345A5A-0238-4AFC-92DB-22F914375626
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33568024-46345A5A-0238-4AFC-92DB-22F914375626
rank
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type
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wasDerivedFrom
f7cb72fb6498cbdb2b05ef8ac38e7698348b3a41
P2860
Substrate reduction therapy: miglustat as a remedy for symptomatic patients with Gaucher disease type 1.