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Q34621690-EA3477E0-ADF9-474C-AFFB-4E6AD3245B6A
Q34621690-EA3477E0-ADF9-474C-AFFB-4E6AD3245B6A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34621690-EA3477E0-ADF9-474C-AFFB-4E6AD3245B6A
Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I
P2860
Q34621690-EA3477E0-ADF9-474C-AFFB-4E6AD3245B6A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34621690-EA3477E0-ADF9-474C-AFFB-4E6AD3245B6A
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type
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Statement
wasDerivedFrom
985df90839611566074b1d9fc9521680e60cc036
P2860
A self-inactivating gamma-retroviral vector reduces manifestations of mucopolysaccharidosis I in mice