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Q34985010-BFF107A3-2DBF-4951-9B28-CC3810F8172D
Q34985010-BFF107A3-2DBF-4951-9B28-CC3810F8172D
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http://www.wikidata.org/entity/statement/Q34985010-BFF107A3-2DBF-4951-9B28-CC3810F8172D
Candidate molecules for chemical chaperone therapy of GM1-gangliosidosis.
P2860
Q34985010-BFF107A3-2DBF-4951-9B28-CC3810F8172D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34985010-BFF107A3-2DBF-4951-9B28-CC3810F8172D
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c3823be20ac8f92cc78070027bf89976d3029302
P2860
Evaluation of N-nonyl-deoxygalactonojirimycin as a pharmacological chaperone for human GM1 gangliosidosis leads to identification of a feline model suitable for testing enzyme enhancement therapy.