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Q35029971-1C4D3D4F-F020-4D01-9C7D-1CE39A77B549
Q35029971-1C4D3D4F-F020-4D01-9C7D-1CE39A77B549
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Statement
http://www.wikidata.org/entity/statement/Q35029971-1C4D3D4F-F020-4D01-9C7D-1CE39A77B549
Pompe disease: literature review and case series
P2860
Q35029971-1C4D3D4F-F020-4D01-9C7D-1CE39A77B549
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35029971-1C4D3D4F-F020-4D01-9C7D-1CE39A77B549
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f7c433786888c53255ed957f3be7ccb132e1dc49
P2860
Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.