Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.
about
Targeted approaches to induce immune tolerance for Pompe disease therapyRetrograde gene delivery to hypoglossal motoneurons using adeno-associated virus serotype 9.Targeted delivery of TrkB receptor to phrenic motoneurons enhances functional recovery of rhythmic phrenic activity after cervical spinal hemisection.Pompe disease: literature review and case seriesComparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe miceCorrecting Neuromuscular Deficits With Gene Therapy in Pompe DiseaseDiaphragm and ventilatory dysfunction during cancer cachexia.Intrapleural administration of AAV9 improves neural and cardiorespiratory function in Pompe disease.B-Cell depletion and immunomodulation before initiation of enzyme replacement therapy blocks the immune response to acid alpha-glucosidase in infantile-onset Pompe disease.The respiratory neuromuscular system in Pompe disease.Histopathological Evaluation of Skeletal Muscle with Specific Reference to Mouse Models of Muscular Dystrophy.Combination Therapies for Lysosomal Storage Diseases: A Complex Answer to a Simple Problem.Transcriptome assessment of the Pompe (Gaa-/-) mouse spinal cord indicates widespread neuropathology.Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.AAV gene delivery to the spinal cord: serotypes, methods, candidate diseases, and clinical trials.
P2860
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P2860
Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.
description
2011 nî lūn-bûn
@nan
2011年の論文
@ja
2011年論文
@yue
2011年論文
@zh-hant
2011年論文
@zh-hk
2011年論文
@zh-mo
2011年論文
@zh-tw
2011年论文
@wuu
2011年论文
@zh
2011年论文
@zh-cn
name
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@ast
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@en
type
label
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@ast
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@en
prefLabel
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@ast
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@en
P2093
P2860
P356
P1433
P1476
Spinal delivery of AAV vector ...... ses ventilation in Pompe mice.
@en
P2093
Barry J Byrne
Darin J Falk
David D Fuller
Paul J Reier
P2860
P356
10.1038/MT.2011.214
P577
2011-10-18T00:00:00Z