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Q35600316-8A2C24F5-ED50-421E-AF85-A109BCCBA588
Q35600316-8A2C24F5-ED50-421E-AF85-A109BCCBA588
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35600316-8A2C24F5-ED50-421E-AF85-A109BCCBA588
Normalization and improvement of CNS deficits in mice with Hurler syndrome after long-term peripheral delivery of BBB-targeted iduronidase.
P2860
Q35600316-8A2C24F5-ED50-421E-AF85-A109BCCBA588
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35600316-8A2C24F5-ED50-421E-AF85-A109BCCBA588
rank
NormalRank
type
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Statement
wasDerivedFrom
e6f3b51433d4b52f9b2e47dd59ba33341b4ac1bd
P2860
Co-expression of MGMT(P140K) and alpha-L-iduronidase in primary hepatocytes from mucopolysaccharidosis type I mice enables efficient selection with metabolic correction.