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Q35665212-2AEEA6B1-DAA8-42BF-8DAD-5745E9E08782
Q35665212-2AEEA6B1-DAA8-42BF-8DAD-5745E9E08782
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35665212-2AEEA6B1-DAA8-42BF-8DAD-5745E9E08782
Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.
P2860
Q35665212-2AEEA6B1-DAA8-42BF-8DAD-5745E9E08782
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35665212-2AEEA6B1-DAA8-42BF-8DAD-5745E9E08782
rank
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Statement
wasDerivedFrom
f3ca4e11118b2bf0cc8fa3bbf330d67b0303ac44
P2860
Long-term clinical improvement in MPTP-lesioned primates after gene therapy with AAV-hAADC.