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Q35903220-8DA7C7A1-812B-410E-8C87-4ECD4F71B51C
Q35903220-8DA7C7A1-812B-410E-8C87-4ECD4F71B51C
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Statement
http://www.wikidata.org/entity/statement/Q35903220-8DA7C7A1-812B-410E-8C87-4ECD4F71B51C
Correcting Neuromuscular Deficits With Gene Therapy in Pompe Disease
P2860
Q35903220-8DA7C7A1-812B-410E-8C87-4ECD4F71B51C
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35903220-8DA7C7A1-812B-410E-8C87-4ECD4F71B51C
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ca424f8b8375acf25e8283c6699f58af2338f963
P2860
Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.