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Q36164927-0B4FC377-CFEE-4293-B01D-70FDF8D93D6F
Q36164927-0B4FC377-CFEE-4293-B01D-70FDF8D93D6F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36164927-0B4FC377-CFEE-4293-B01D-70FDF8D93D6F
Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.
P2860
Q36164927-0B4FC377-CFEE-4293-B01D-70FDF8D93D6F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36164927-0B4FC377-CFEE-4293-B01D-70FDF8D93D6F
rank
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type
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wasDerivedFrom
4c04364e1a83d0b11debef320912f51c848bbb51
P2860
Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D.