Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.
about
Targeted approaches to induce immune tolerance for Pompe disease therapyIn vivo tissue-tropism of adeno-associated viral vectors.Progress toward Gene Therapy for Duchenne Muscular Dystrophy.Complexity of immune responses to AAV transgene products - Example of factor IX.Prolonged Expression of Secreted Enzymes in Dogs After Liver-Directed Delivery of Sleeping Beauty Transposons: Implications for Non-Viral Gene Therapy of Systemic Disease.Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in children affected by Pompe Disease.The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute.Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase.Emerging Issues in AAV-Mediated In Vivo Gene Therapy.Safety First: Perspective on Patient-Centered Development of AAV Gene Therapy Products.Gene Therapy With Regulatory T Cells: A Beneficial Alliance.Mapping an Adeno-associated Virus 9-Specific Neutralizing Epitope To Develop Next-Generation Gene Delivery Vectors
P2860
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P2860
Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
Evaluation of Readministration ...... clinical to Clinical Planning.
@ast
Evaluation of Readministration ...... clinical to Clinical Planning.
@en
type
label
Evaluation of Readministration ...... clinical to Clinical Planning.
@ast
Evaluation of Readministration ...... clinical to Clinical Planning.
@en
prefLabel
Evaluation of Readministration ...... clinical to Clinical Planning.
@ast
Evaluation of Readministration ...... clinical to Clinical Planning.
@en
P2093
P2860
P356
P1476
Evaluation of Readministration ...... clinical to Clinical Planning.
@en
P2093
Alice F Tarantal
Barry J Byrne
Brian Cleaver
Davis Fuller
Gensheng Wang
Janet Benson
Kaitlyn J Faris
Manuela Corti
Nathalie Clément
Roland W Herzog
P2860
P304
P356
10.1089/HUMC.2015.068
P577
2015-09-01T00:00:00Z