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Q36164927-44C739DE-F0B0-44B6-B94B-5BFF75DE3A21
Q36164927-44C739DE-F0B0-44B6-B94B-5BFF75DE3A21
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36164927-44C739DE-F0B0-44B6-B94B-5BFF75DE3A21
Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.
P2860
Q36164927-44C739DE-F0B0-44B6-B94B-5BFF75DE3A21
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36164927-44C739DE-F0B0-44B6-B94B-5BFF75DE3A21
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Statement
wasDerivedFrom
a20bd447acfa5b32fc64d61e43b3c9aee9d1cc55
P2860
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years.