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Q39404266-727E91EF-1B19-4A83-B72C-DD4948974001
Q39404266-727E91EF-1B19-4A83-B72C-DD4948974001
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39404266-727E91EF-1B19-4A83-B72C-DD4948974001
Transcriptome assessment of the Pompe (Gaa-/-) mouse spinal cord indicates widespread neuropathology.
P2860
Q39404266-727E91EF-1B19-4A83-B72C-DD4948974001
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39404266-727E91EF-1B19-4A83-B72C-DD4948974001
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7d2998b306fdf5368dd48a6a47396095326dc142
P2860
Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.