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Q41574484-F8A2258C-152F-476C-8194-57462FE773CB
Q41574484-F8A2258C-152F-476C-8194-57462FE773CB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41574484-F8A2258C-152F-476C-8194-57462FE773CB
A bicyclic 1-deoxygalactonojirimycin derivative as a novel pharmacological chaperone for GM1 gangliosidosis.
P2860
Q41574484-F8A2258C-152F-476C-8194-57462FE773CB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41574484-F8A2258C-152F-476C-8194-57462FE773CB
rank
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type
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Statement
wasDerivedFrom
a8374e0c5f71753bc6c4c431c8e4ac26450825be
P2860
Evaluation of N-nonyl-deoxygalactonojirimycin as a pharmacological chaperone for human GM1 gangliosidosis leads to identification of a feline model suitable for testing enzyme enhancement therapy.