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Q41625013-8A44DFCB-119C-4D58-A8CC-3AADA0DF7D30
Q41625013-8A44DFCB-119C-4D58-A8CC-3AADA0DF7D30
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Statement
http://www.wikidata.org/entity/statement/Q41625013-8A44DFCB-119C-4D58-A8CC-3AADA0DF7D30
Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.
P2860
Q41625013-8A44DFCB-119C-4D58-A8CC-3AADA0DF7D30
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41625013-8A44DFCB-119C-4D58-A8CC-3AADA0DF7D30
rank
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wasDerivedFrom
71712204b0940c34cc431c941358bcb1242e02f8
P2860
Spinal delivery of AAV vector restores enzyme activity and increases ventilation in Pompe mice.