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Q44016335-62D33165-F18C-4E56-87C0-288934794C3B
Q44016335-62D33165-F18C-4E56-87C0-288934794C3B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q44016335-62D33165-F18C-4E56-87C0-288934794C3B
In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.
P2860
Q44016335-62D33165-F18C-4E56-87C0-288934794C3B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q44016335-62D33165-F18C-4E56-87C0-288934794C3B
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Statement
wasDerivedFrom
c8a65b6eb0cf8cff49b4cef725729ccf7cbef98c
P2860
Mutational analysis of 85 mucopolysaccharidosis type I families: frequency of known mutations, identification of 17 novel mutations and in vitro expression of missense mutations.