In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

about

Collagen alpha1(I) gene (COL1A1) is repressed by RFX family Treatment of the mouse model of mucopolysaccharidosis type IIIB with lentiviral-NAGLU vector.

P2860

Q40443136-DF23778F-4607-4749-8B35-E9F12D1BEFA4 Q42229261-D3106B79-E689-42D8-84A6-6329509622FA

P2860

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

Item

http://www.wikidata.org/entity/Q44016335

description

2002 nî lūn-bûn

@nan

2002年の論文

@ja

2002年学术文章

@wuu

2002年学术文章

@zh

2002年学术文章

@zh-cn

2002年学术文章

@zh-hans

2002年学术文章

@zh-my

2002年学术文章

@zh-sg

2002年學術文章

@yue

2002年學術文章

@zh-hant

name

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@en

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@nl

type

Item

label

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@en

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@nl

prefLabel

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@en

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@nl

P1476

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

@en

P2093

Carmela Di Domenico

http://www.w3.org/2001/XMLSchema#string

Guglielmo R D Villani

http://www.w3.org/2001/XMLSchema#string

Paola Di Natale

http://www.w3.org/2001/XMLSchema#string

P2860

Structure and sequence of the human alpha-L-iduronidase gene

Murine mucopolysaccharidosis type I: targeted disruption of the murine alpha-L-iduronidase gene

Human alpha-L-iduronidase: cDNA isolation and expression

The biogenesis of lysosomes

Clinical gene therapy in hematology: past and future.

Bone marrow transplantation for mucopolysaccharidosis type I: experience of two British centres.

Long-term in vitro correction of alpha-L-iduronidase deficiency (Hurler syndrome) in human bone marrow.

A fluorometric assay using 4-methylumbelliferyl alpha-L-iduronide for the estimation of alpha-L-iduronidase activity and the detection of Hurler and Scheie syndromes.

Retroviral vector design studies toward hematopoietic stem cell gene therapy for mucopolysaccharidosis type I.

Characterization of novel safe lentiviral vectors derived from simian immunodeficiency virus (SIVmac251) that efficiently transduce mature human dendritic cells.

P304

2764-2771

http://www.w3.org/2001/XMLSchema#string

P31

scholarly article

P356

10.1046/J.1432-1033.2002.02951.X

http://www.w3.org/2001/XMLSchema#string

P407

English

P433

http://www.w3.org/2001/XMLSchema#string

P478

269

http://www.w3.org/2001/XMLSchema#string

P50

Luigi Naldini

Antonia Follenzi

Angelo Leone Lombardo

P577

2002-06-01T00:00:00Z

http://www.w3.org/2001/XMLSchema#dateTime

P5875

11326770

http://www.w3.org/2001/XMLSchema#string

P698

12047386

http://www.w3.org/2001/XMLSchema#string

P921

gene therapy

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

about

P2860

P2860

In vitro gene therapy of mucopolysaccharidosis type I by lentiviral vectors.

description

name

type

label

prefLabel

P1433

P1476

P2093

P2860

P304

P31

P356

P407

P433

P478

P50

P577

P5875

P698

P921

P356

P1433

P1476

P2093

P2860

P304

P31

P356

P407

P433

P478

P50

P577

P5875

P698

P921