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Q45324511-859DE9AE-DF18-419D-AB88-9BCD5A26429E
Q45324511-859DE9AE-DF18-419D-AB88-9BCD5A26429E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45324511-859DE9AE-DF18-419D-AB88-9BCD5A26429E
Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in children affected by Pompe Disease.
P2860
Q45324511-859DE9AE-DF18-419D-AB88-9BCD5A26429E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45324511-859DE9AE-DF18-419D-AB88-9BCD5A26429E
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
00875f9897a78154941b67564bde19fff7557f54
P2860
Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning.