Correction of the UDP-glucuronosyltransferase gene defect in the gunn rat model of crigler-najjar syndrome type I with a chimeric oligonucleotide
about
Lifelong elimination of hyperbilirubinemia in the Gunn rat with a single injection of helper-dependent adenoviral vectorA trial of somatic gene targeting in vivo with an adenovirus vector.Genetic spell-checking: gene editing using single-stranded DNA oligonucleotidesGenetic lesions of bilirubin uridine-diphosphoglucuronate glucuronosyltransferase (UGT1A1) causing Crigler-Najjar and Gilbert syndromes: correlation of genotype to phenotypeOligo/polynucleotide-based gene modification: strategies and therapeutic potentialGene correction of the apolipoprotein (Apo) E2 phenotype to wild-type ApoE3 by in situ chimeraplasty.Rad51p and Rad54p, but not Rad52p, elevate gene repair in Saccharomyces cerevisiae directed by modified single-stranded oligonucleotide vectors.In vivo gene delivery to the lung using polyethylenimine and fractured polyamidoamine dendrimers.The potential of nucleic acid repair in functional genomics.From gene transfer to gene therapy in lysosomal storage diseases affecting the central nervous system.Long-term reduction of jaundice in Gunn rats by nonviral liver-targeted delivery of Sleeping Beauty transposonTherapeutic application of chimeric RNA/DNA oligonucleotide based gene therapy.RNase P: variations and uses.Gene therapy for haemophilia.Gene repair in the new age of gene therapy.Pediatric liver transplantation in metabolic disease: clinical decision making.Optimizing the delivery systems of chimeric RNA.DNA oligonucleotides.Adeno-associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo.The development and regulation of gene repair.Targeted gene repair -- in the arena.Engineered ribozymes as molecular tools for site-specific alteration of RNA sequence.Gene therapy of liver diseases.Applications of gene therapy for familial amyloidotic polyneuropathy.Targeted In Situ Gene Correction of Dysfunctional APOE Alleles to Produce Atheroprotective Plasma ApoE3 Protein.Cloning of UGT1A9 cDNA from liver tissues and its expression in CHL cells.Rescue of dystrophin expression in mdx mouse muscle by RNA/DNA oligonucleotides.Liver cell transplantation for Crigler-Najjar syndrome type I: update and perspectives.Gene therapy for liver enzyme deficiencies: what have we learned from models for Crigler-Najjar and tyrosinemia?'Smart' non-viral delivery systems for targeted delivery of RNAi to the lungs.Emerging gene editing strategies for Duchenne muscular dystrophy targeting stem cells.Targeted gene repair in mammalian cells using chimeric RNA/DNA oligonucleotides and modified single-stranded vectors.In vitro and in vivo nucleotide exchange directed by chimeric RNA/DNA oligonucleotides in Saccharomyces cerevisae.Gene-targeting pharmaceuticals for single-gene disorders.Developmental, Genetic, Dietary, and Xenobiotic Influences on Neonatal Hyperbilirubinemia.In vivo gene repair of point and frameshift mutations directed by chimeric RNA/DNA oligonucleotides and modified single-stranded oligonucleotides.Strand bias in targeted gene repair is influenced by transcriptional activity.Non-viral vector-mediated uptake, distribution, and stability of chimeraplasts in human airway epithelial cells.Single-stranded oligonucleotide-mediated in vivo gene repair in the rd1 retina.Summary report of a symposium: genes and gene delivery for diseases of alcoholism.Chimeric RNA/DNA oligonucleotide-based site-specific modification of the tobacco acetolactate syntase gene.
P2860
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P2860
Correction of the UDP-glucuronosyltransferase gene defect in the gunn rat model of crigler-najjar syndrome type I with a chimeric oligonucleotide
description
1999 nî lūn-bûn
@nan
1999年の論文
@ja
1999年論文
@yue
1999年論文
@zh-hant
1999年論文
@zh-hk
1999年論文
@zh-mo
1999年論文
@zh-tw
1999年论文
@wuu
1999年论文
@zh
1999年论文
@zh-cn
name
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@ast
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@en
type
label
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@ast
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@en
prefLabel
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@ast
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@en
P2093
P2860
P356
P1476
Correction of the UDP-glucuron ...... ith a chimeric oligonucleotide
@en
P2093
B Parashar
J R Chowdhury
N R Chowdhury
P Bandyopadhyay
P2860
P304
10349-10354
P356
10.1073/PNAS.96.18.10349
P407
P577
1999-08-01T00:00:00Z