2004 William Allan Award address. Cloning of the DMD gene.
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Marginal level dystrophin expression improves clinical outcome in a strain of dystrophin/utrophin double knockout miceQuantitative phenotyping of Duchenne muscular dystrophy dogs by comprehensive gait analysis and overnight activity monitoringAnimal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapySystemic Trans-splicing adeno-associated viral delivery efficiently transduces the heart of adult mdx mouse, a model for duchenne muscular dystrophySarcolemmal nNOS anchoring reveals a qualitative difference between dystrophin and utrophin.Adeno-associated virus serotype-9 microdystrophin gene therapy ameliorates electrocardiographic abnormalities in mdx mice.iNOS ablation does not improve specific force of the extensor digitorum longus muscle in dystrophin-deficient mdx4cv mice.Systemic gene transfer reveals distinctive muscle transduction profile of tyrosine mutant AAV-1, -6, and -9 in neonatal dogs.Nitrosative stress elicited by nNOSµ delocalization inhibits muscle force in dystrophin-null miceDuchenne muscular dystrophy gene therapy: Lost in translation?Characterization of 65 epitope-specific dystrophin monoclonal antibodies in canine and murine models of duchenne muscular dystrophy by immunostaining and western blot.The FVB Background Does Not Dramatically Alter the Dystrophic Phenotype of Mdx MiceDuchenne muscular dystrophy gene therapy in the canine model.Novel mini-dystrophin gene dual adeno-associated virus vectors restore neuronal nitric oxide synthase expression at the sarcolemmaA simplified immune suppression scheme leads to persistent micro-dystrophin expression in Duchenne muscular dystrophy dogsGender differences in contractile and passive properties of mdx extensor digitorum longus muscle.Safe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus.Perspective on Adeno-Associated Virus Capsid Modification for Duchenne Muscular Dystrophy Gene TherapyAbsence of Dystrophin Disrupts Skeletal Muscle Signaling: Roles of Ca2+, Reactive Oxygen Species, and Nitric Oxide in the Development of Muscular Dystrophy.α2 and α3 helices of dystrophin R16 and R17 frame a microdomain in the α1 helix of dystrophin R17 for neuronal NOS binding.Preservation of muscle force in Mdx3cv mice correlates with low-level expression of a near full-length dystrophin proteinFrom the smallest virus to the biggest gene: marching towards gene therapy for duchenne muscular dystrophy.Prospect of gene therapy for cardiomyopathy in hereditary muscular dystrophy.Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.Dual AAV therapy ameliorates exercise-induced muscle injury and functional ischemia in murine models of Duchenne muscular dystrophySub-physiological sarcoglycan expression contributes to compensatory muscle protection in mdx miceGenomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotypeDual AAV gene therapy for Duchenne muscular dystrophy with a 7-kb mini-dystrophin gene in the canine model.Uniform low-level dystrophin expression in the heart partially preserved cardiac function in an aged mouse model of Duchenne cardiomyopathy.Reassessing carrier status for dystrophinopathies.Dystrophin Gene Replacement and Gene Repair Therapy for Duchenne Muscular Dystrophy in 2016: An Interview.The postoperative cardiovascular arrest of a 5-year-old male: an initial presentation of Duchenne's muscular dystrophy.Micro-dystrophin gene therapy goes systemic in Duchenne muscular dystrophy patients.A Postgenomic Perspective on Molecular Cytogenetics.Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy
P2860
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P2860
2004 William Allan Award address. Cloning of the DMD gene.
description
2005 nî lūn-bûn
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2005 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2005 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2005年の論文
@ja
2005年論文
@yue
2005年論文
@zh-hant
2005年論文
@zh-hk
2005年論文
@zh-mo
2005年論文
@zh-tw
2005年论文
@wuu
name
2004 William Allan Award address. Cloning of the DMD gene.
@ast
2004 William Allan Award address. Cloning of the DMD gene.
@en
type
label
2004 William Allan Award address. Cloning of the DMD gene.
@ast
2004 William Allan Award address. Cloning of the DMD gene.
@en
prefLabel
2004 William Allan Award address. Cloning of the DMD gene.
@ast
2004 William Allan Award address. Cloning of the DMD gene.
@en
P2860
P356
P1476
2004 William Allan Award address. Cloning of the DMD gene.
@en
P2093
Louis M Kunkel
P2860
P304
P356
10.1086/428143
P407
P577
2005-02-01T00:00:00Z