Correction of glucocerebrosidase deficiency after retroviral-mediated gene transfer into hematopoietic progenitor cells from patients with Gaucher disease.
about
Hematopoietic stem cell gene therapy:assessing the relevance of preclinical modelsMurine models of acute neuronopathic Gaucher disease.Effective cell and gene therapy in a murine model of Gaucher disease.Selection of transduced CD34+ progenitors and enzymatic correction of cells from Gaucher patients, with bicistronic vectorsLong-term in vivo expression of the human glucocerebrosidase gene in nonhuman primates after CD34+ hematopoietic cell transduction with cell-free retroviral vector preparations.Retroviral-mediated transfer of the human glucocerebrosidase gene into cultured Gaucher bone marrow.Metabolic correction and cross-correction of mucopolysaccharidosis type II (Hunter syndrome) by retroviral-mediated gene transfer and expression of human iduronate-2-sulfataseβ-Glucosidase 2 (GBA2) activity and imino sugar pharmacology.Acid beta-glucosidase: enzymology and molecular biology of Gaucher disease.Gaucher disease: Progress and ongoing challenges.Induced Pluripotent Stem Cell Modeling of Gaucher's Disease: What Have We Learned?Non-viral, integrin-mediated gene transfer into fibroblasts from patients with lysosomal storage diseases.Restoration of arylsulphatase B activity in human mucopolysaccharidosis-type-VI fibroblasts by retroviral-vector-mediated gene transfer.VP22 enhances the expression of glucocerebrosidase in human Gaucher II fibroblast cells mediated by lentiviral vectors.Gaucher disease
P2860
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P2860
Correction of glucocerebrosidase deficiency after retroviral-mediated gene transfer into hematopoietic progenitor cells from patients with Gaucher disease.
description
1990 nî lūn-bûn
@nan
1990 թուականի Մարտին հրատարակուած գիտական յօդուած
@hyw
1990 թվականի մարտին հրատարակված գիտական հոդված
@hy
1990年の論文
@ja
1990年論文
@yue
1990年論文
@zh-hant
1990年論文
@zh-hk
1990年論文
@zh-mo
1990年論文
@zh-tw
1990年论文
@wuu
name
Correction of glucocerebrosida ...... patients with Gaucher disease.
@ast
Correction of glucocerebrosida ...... patients with Gaucher disease.
@en
Correction of glucocerebrosida ...... patients with Gaucher disease.
@nl
type
label
Correction of glucocerebrosida ...... patients with Gaucher disease.
@ast
Correction of glucocerebrosida ...... patients with Gaucher disease.
@en
Correction of glucocerebrosida ...... patients with Gaucher disease.
@nl
prefLabel
Correction of glucocerebrosida ...... patients with Gaucher disease.
@ast
Correction of glucocerebrosida ...... patients with Gaucher disease.
@en
Correction of glucocerebrosida ...... patients with Gaucher disease.
@nl
P2093
P2860
P356
P1476
Correction of glucocerebrosida ...... patients with Gaucher disease.
@en
P2093
P2860
P304
P356
10.1073/PNAS.87.6.2334
P407
P577
1990-03-01T00:00:00Z