AAV hybrid serotypes: improved vectors for gene delivery
about
Advanced In vivo Use of CRISPR/Cas9 and Anti-sense DNA Inhibition for Gene Manipulation in the BrainMorquio A syndrome: diagnosis and current and future therapiesDisease rescue and increased lifespan in a model of cardiomyopathy and muscular dystrophy by combined AAV treatmentsElectron microscopy analysis of a disaccharide analog complex reveals receptor interactions of adeno-associated virusTransferrin-mediated targeting of bacteriophage HK97 nanoparticles into tumor cells.Interior engineering of a viral nanoparticle and its tumor homing properties.In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses.Engineering and selection of shuffled AAV genomes: a new strategy for producing targeted biological nanoparticles.Efficient intrathymic gene transfer following in situ administration of a rAAV serotype 8 vector in mice and nonhuman primates.Establishment of an AAV reverse infection-based array.Viral vectors for neurotrophic factor delivery: a gene therapy approach for neurodegenerative diseases of the CNSGene therapy for inherited muscle diseases: where genetics meets rehabilitation medicine.Therapies of mucopolysaccharidosis IVA (Morquio A syndrome).Alpha2,3 and alpha2,6 N-linked sialic acids facilitate efficient binding and transduction by adeno-associated virus types 1 and 6Recombinant AAV-directed gene therapy for type I glycogen storage diseases.Enhanced real-time monitoring of adeno-associated virus trafficking by virus-quantum dot conjugatesHost cell DNA repair pathways in adeno-associated viral genome processingSingle amino acid changes can influence titer, heparin binding, and tissue tropism in different adeno-associated virus serotypes.Perspectives on the use of gene therapy for chronic joint diseases.Enhancing gene delivery of adeno-associated viruses by cell-permeable peptidesAdeno-associated virus type 2 vectors: transduction and long-term expression in cerebellar Purkinje cells in vivo is mediated by the fibroblast growth factor receptor 1 : bFGFR-1 mediates AAV2 transduction of Purkinje cells.Notch1 augments intracellular trafficking of adeno-associated virus type 2.Vectored antibody gene delivery for the prevention or treatment of HIV infection.Methods for gene transfer to the central nervous system.The threefold protrusions of adeno-associated virus type 8 are involved in cell surface targeting as well as postattachment processing.New vectors and strategies for cardiovascular gene therapy.Gene therapy progress and prospects--vectorology: design and production of expression cassettes in AAV vectors.Nanoparticle-motivated gene delivery for ophthalmic applicationSerotype-dependent transduction efficiencies of recombinant adeno-associated viral vectors in monkey neocortexA survey of ex vivo/in vitro transduction efficiency of mammalian primary cells and cell lines with Nine natural adeno-associated virus (AAV1-9) and one engineered adeno-associated virus serotypeThe use of recombinant adeno-associated virus for skeletal gene therapy.The neostriatum: two entities, one structure?Gene therapy for type I glycogen storage diseasesCrystallization and preliminary X-ray structural studies of adeno-associated virus serotype 6Adeno-associated viral vectors show serotype specific transduction of equine joint tissue explants and cultured monolayersThe state of the art of adeno-associated virus-based vectors in gene therapy.Bioengineering of AAV2 capsid at specific serine, threonine, or lysine residues improves its transduction efficiency in vitro and in vivo.Targeted modifications in adeno-associated virus serotype 8 capsid improves its hepatic gene transfer efficiency in vivoGPR30 differentially regulates short latency responses of luteinising hormone and prolactin secretion to oestradiolSelection and evaluation of clinically relevant AAV variants in a xenograft liver model.
P2860
Q26770355-95D527FC-CF32-4316-9461-307FCB330D6DQ27014063-B38068C7-0FB1-4005-B950-08765D0E9A6AQ27349992-E2A9A385-6227-463E-8F4F-54326E240322Q27679952-92CBF030-B454-4C1D-A00A-420C678B2257Q30500177-5803E21D-5642-409C-8D9A-1C77F0D4CFABQ30530235-933B77EE-A582-44E8-AB00-EF8339B86BA3Q33327474-0E9E45AA-1CF1-40F0-847A-456084115C7FQ33337378-D3AE5642-F31A-421D-889B-7DF414237C18Q33713355-CD38DC1E-58A8-4F64-86FA-C9B4C0DBB3EDQ33728191-D16A27DB-300B-4111-AD13-EB3421F1A020Q33894621-F0D94715-270F-4E5D-B2DC-47F6ECDE0E4EQ34340857-753EFD4A-767A-4537-BACC-A98B52B8FBA7Q34545883-8A59DEF4-EDFD-4EA3-ABC2-15B4BD2198F1Q35024289-773C6913-18D2-40D2-BD34-57BFB6B8D44BQ35078590-08F296BC-5C33-4EEF-AFA1-0CACAA875DA5Q35094530-F38F4F96-C215-4AC0-9924-673CCCE59381Q35139314-AFDAEF33-9379-418F-867F-69FB2C9C16ACQ35139648-CC31C045-9D5B-49EE-9148-850C4E8576F4Q35151031-0B82C8B1-6D43-45A9-8936-09915C3680D6Q35194907-8E355E66-FBB4-42D2-936B-41306C65BECCQ35362227-CC5E8554-143A-4C9C-A2FA-0C2B3929BD5DQ35635454-B1644BF5-2A6F-424C-ABD7-F5CCB7ADDF45Q35664155-A7F99098-7151-4E64-B68A-2B620C5D7A1DQ35902332-2024234F-A8A4-42B6-AAA0-133C728C31F9Q36155013-71365B45-A18F-4D52-911A-9B727BF2AA24Q36174173-5BAC397C-3937-4507-88CC-049D0A79EEB2Q36384464-141395E3-B66A-4D4A-8F99-38DD829B5AAEQ36396201-D61E58BB-1157-4F4F-A6CF-26260584408FQ36508670-B3C02D29-8E5B-4D93-8F61-FABF40C0F7EEQ36715338-32DDC98D-8137-46A6-AAEE-FFBC9283455CQ36729692-E5650FEB-6418-4B13-AEF0-4ACC6AB1181BQ36762445-862D9058-65B7-4F2C-9719-64470581ADA2Q36789527-896AE29A-8529-46AD-841F-F263C18D2DE4Q36968803-74C096E3-633C-4EF2-A27F-77A5CFE4A4F0Q36972596-709D0677-94C1-49BC-B9B0-0C78CC33883DQ36972714-81000D6B-360C-42C9-BAD8-B9A09C03F9D1Q37066323-26778496-8D71-478B-B1A7-A38FB073703BQ37066326-EBE71B5F-D56E-46AB-8CD4-1AF919C70D86Q37373591-5BD366D3-8010-44AC-BB7F-AAAE60B66983Q37610916-353BF044-735B-4944-89A7-74C10EE2D5D8
P2860
AAV hybrid serotypes: improved vectors for gene delivery
description
2005 nî lūn-bûn
@nan
2005 թուականի Յունիսին հրատարակուած գիտական յօդուած
@hyw
2005 թվականի հունիսին հրատարակված գիտական հոդված
@hy
2005年の論文
@ja
2005年論文
@yue
2005年論文
@zh-hant
2005年論文
@zh-hk
2005年論文
@zh-mo
2005年論文
@zh-tw
2005年论文
@wuu
name
AAV hybrid serotypes: improved vectors for gene delivery
@ast
AAV hybrid serotypes: improved vectors for gene delivery
@en
AAV hybrid serotypes: improved vectors for gene delivery
@nl
type
label
AAV hybrid serotypes: improved vectors for gene delivery
@ast
AAV hybrid serotypes: improved vectors for gene delivery
@en
AAV hybrid serotypes: improved vectors for gene delivery
@nl
prefLabel
AAV hybrid serotypes: improved vectors for gene delivery
@ast
AAV hybrid serotypes: improved vectors for gene delivery
@en
AAV hybrid serotypes: improved vectors for gene delivery
@nl
P2093
P2860
P356
P1433
P1476
AAV hybrid serotypes: improved vectors for gene delivery
@en
P2093
Douglas M McCarty
R Jude Samulski
Vivian W Choi
P2860
P304
P356
10.2174/1566523054064968
P407
P577
2005-06-01T00:00:00Z