Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.
about
Cilia in vertebrate development and diseaseGene therapy of inherited retinal degenerations: prospects and challengesA comprehensive review of retinal gene therapyEffects of Pathogenic Variations in the Human Rhodopsin Gene (hRHO) on the Predicted Accessibility for a Lead Candidate Ribozyme.Rescue of photoreceptor degeneration by curcumin in transgenic rats with P23H rhodopsin mutation.Vector platforms for gene therapy of inherited retinopathies.The domestic cat as a large animal model for characterization of disease and therapeutic intervention in hereditary retinal blindness.AAV delivery of wild-type rhodopsin preserves retinal function in a mouse model of autosomal dominant retinitis pigmentosa.Variables and strategies in development of therapeutic post-transcriptional gene silencing agentsGenotypic and phenotypic characterization of P23H line 1 rat model.A Novel, Real-Time, In Vivo Mouse Retinal Imaging SystemDevelopment of lead hammerhead ribozyme candidates against human rod opsin mRNA for retinal degeneration therapy.Rapid, cell-based toxicity screen of potentially therapeutic post-transcriptional gene silencing agentsER stress is involved in T17M rhodopsin-induced retinal degeneration.Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients.Reduction in severity of a herpes simplex virus type 1 murine infection by treatment with a ribozyme targeting the UL20 gene RNA.Nanoparticle applications in ocular gene therapyRescue of sight by gene therapy - closer than it may appear.AAV vectors for RNA-based modulation of gene expression.Allele-Specific Inhibition of Rhodopsin With an Antisense Oligonucleotide Slows Photoreceptor Cell DegenerationAdvances in gene therapy technologies to treat retinitis pigmentosa.The use of canine models of inherited retinal degeneration to test novel therapeutic approaches.Progress toward effective treatments for human photoreceptor degenerations.Gene therapy in the Retinal Degeneration Slow model of retinitis pigmentosa.Gene-based therapies for dominantly inherited retinopathies.Gene therapy in animal models of autosomal dominant retinitis pigmentosaGene therapies for inherited retinal disorders.Improved retinal function in a mouse model of dominant retinitis pigmentosa following AAV-delivered gene therapy.A cellular high-throughput screening approach for therapeutic trans-cleaving ribozymes and RNAi against arbitrary mRNA disease targets.Long-term rescue of retinal structure and function by rhodopsin RNA replacement with a single adeno-associated viral vector in P23H RHO transgenic mice.Mutation-independent rescue of a novel mouse model of Retinitis PigmentosaGene delivery of wild-type rhodopsin rescues retinal function in an autosomal dominant retinitis pigmentosa mouse model.Discordant anatomical, electrophysiological, and visual behavioral profiles of retinal degeneration in rat models of retinal degenerative disease.RNA interference-mediated suppression and replacement of human rhodopsin in vivo.In vitro analysis of ribozyme-mediated knockdown of an ADRP associated rhodopsin mutation.AAV-mediated knockdown of peripherin-2 in vivo using miRNA-based hairpins.Phenotypic characterization of P23H and S334ter rhodopsin transgenic rat models of inherited retinal degeneration.Clustered Regularly Interspaced Short Palindromic Repeats-Based Genome Surgery for the Treatment of Autosomal Dominant Retinitis Pigmentosa.
P2860
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P2860
Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.
description
2006 nî lūn-bûn
@nan
2006年の論文
@ja
2006年論文
@yue
2006年論文
@zh-hant
2006年論文
@zh-hk
2006年論文
@zh-mo
2006年論文
@zh-tw
2006年论文
@wuu
2006年论文
@zh
2006年论文
@zh-cn
name
Preservation of photoreceptor ...... n allele independent ribozyme.
@ast
Preservation of photoreceptor ...... n allele independent ribozyme.
@en
type
label
Preservation of photoreceptor ...... n allele independent ribozyme.
@ast
Preservation of photoreceptor ...... n allele independent ribozyme.
@en
prefLabel
Preservation of photoreceptor ...... n allele independent ribozyme.
@ast
Preservation of photoreceptor ...... n allele independent ribozyme.
@en
P2860
P50
P1476
Preservation of photoreceptor ...... an allele independent ribozyme
@en
P2093
V Justilien
W W Hauswirth
P2860
P356
10.1016/J.EXER.2006.08.014
P577
2006-11-01T00:00:00Z