Allele-Specific Inhibition of Rhodopsin With an Antisense Oligonucleotide Slows Photoreceptor Cell Degeneration
about
Identification and Correction of Mechanisms Underlying Inherited Blindness in Human iPSC-Derived Optic Cups.Stacking up CRISPR against RNAi for therapeutic gene inhibition.Precision medicine, genomics and drug discovery.In vitro and in vivo rescue of aberrant splicing in CEP290-associated LCA by antisense oligonucleotide delivery.The molecular and cellular basis of rhodopsin retinitis pigmentosa reveals potential strategies for therapy.Phenotypic characterization of P23H and S334ter rhodopsin transgenic rat models of inherited retinal degeneration.Design and In Vitro Use of Antisense Oligonucleotides to Correct Pre-mRNA Splicing Defects in Inherited Retinal Dystrophies.Antisense Therapy for a Common Corneal Dystrophy Ameliorates TCF4 Repeat Expansion-Mediated Toxicity.Identification and Rescue of Splice Defects Caused by Two Neighboring Deep-Intronic ABCA4 Mutations Underlying Stargardt Disease.Antisense Oligonucleotide-Based Splicing Correction in Individuals with Leber Congenital Amaurosis due to Compound Heterozygosity for the c.2991+1655A>G Mutation in CEP290.
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P2860
Allele-Specific Inhibition of Rhodopsin With an Antisense Oligonucleotide Slows Photoreceptor Cell Degeneration
description
article científic
@ca
article scientifique
@fr
articolo scientifico
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artigo científico
@pt
bilimsel makale
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scientific article published on October 2015
@en
vedecký článok
@sk
vetenskaplig artikel
@sv
videnskabelig artikel
@da
vědecký článek
@cs
name
Allele-Specific Inhibition of ...... hotoreceptor Cell Degeneration
@en
Allele-Specific Inhibition of ...... otoreceptor Cell Degeneration.
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type
label
Allele-Specific Inhibition of ...... hotoreceptor Cell Degeneration
@en
Allele-Specific Inhibition of ...... otoreceptor Cell Degeneration.
@nl
prefLabel
Allele-Specific Inhibition of ...... hotoreceptor Cell Degeneration
@en
Allele-Specific Inhibition of ...... otoreceptor Cell Degeneration.
@nl
P2093
P2860
P356
P1476
Allele-Specific Inhibition of ...... hotoreceptor Cell Degeneration
@en
P2093
Ali Jazayeri
Brett P Monia
Douglas Yasumura
Haidong Yang
Matthew M LaVail
Michael L McCaleb
Michael T Matthes
Peter S Adamson
P2860
P304
P356
10.1167/IOVS.15-16400
P407
P577
2015-10-01T00:00:00Z