Mid-stage intervention achieves similar efficacy as conventional early-stage treatment using gene therapy in a pre-clinical model of retinitis pigmentosa

Mid-stage intervention achieves similar efficacy as conventional early-stage treatment using gene therapy in a pre-clinical model of retinitis pigmentosa

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http://www.wikidata.org/entity/Q37406449
Rod Outer Segment Development Influences AAV-Mediated Photoreceptor Transduction After Subretinal Injection.Successful arrest of photoreceptor and vision loss expands the therapeutic window of retinal gene therapy to later stages of disease.Personalized therapeutic strategies for patients with retinitis pigmentosa.CAPN5 gene silencing by short hairpin RNA interference.Gene therapy in patient-specific stem cell lines and a preclinical model of retinitis pigmentosa with membrane frizzled-related protein defects.Advances in Gene Therapy for Diseases of the Eye.Functional validation of a human CAPN5 exome variant by lentiviral transduction into mouse retina.Gene therapies for inherited retinal disorders.Gene and cell-based therapies for inherited retinal disorders: An update.CRISPR Repair Reveals Causative Mutation in a Preclinical Model of Retinitis Pigmentosa.Gene Therapy in a Large Animal Model of PDE6A-Retinitis Pigmentosa.Silencing of tuberin enhances photoreceptor survival and function in a preclinical model of retinitis pigmentosa (an american ophthalmological society thesis).Guiding Lights in Genome Editing for Inherited Retinal Disorders: Implications for Gene and Cell Therapy.Cochlear Gene Therapy for Sensorineural Hearing Loss: Current Status and Major Remaining Hurdles for Translational Success.
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Mid-stage intervention achieves similar efficacy as conventional early-stage treatment using gene therapy in a pre-clinical model of retinitis pigmentosa

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http://www.wikidata.org/entity/Q37406449
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 18 September 2013
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Mid-stage intervention achieve ...... model of retinitis pigmentosa
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Mid-stage intervention achieve ...... model of retinitis pigmentosa.
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Mid-stage intervention achieve ...... model of retinitis pigmentosa
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Mid-stage intervention achieve ...... model of retinitis pigmentosa.
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Mid-stage intervention achieve ...... model of retinitis pigmentosa
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Mid-stage intervention achieve ...... model of retinitis pigmentosa.
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Mid-stage intervention achieve ...... model of retinitis pigmentosa
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