Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
about
Current and future alternative therapies for beta-thalassemia majorCell based therapies for ischemic stroke: from basic science to bedsideβ-thalassemias: paradigmatic diseases for scientific discoveries and development of innovative therapiesCellular function reinstitution of offspring red blood cells cloned from the sickle cell disease patient blood post CRISPR genome editingGene therapy for hemoglobinopathies: the state of the field and the future.Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease.Pigtailed macaques as a model to study long-term safety of lentivirus vector-mediated gene therapy for hemoglobinopathies.Amelioration of murine sickle cell disease by nonablative conditioning and γ-globin gene-corrected bone marrow cells.Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.Treating hemoglobinopathies using gene-correction approaches: promises and challenges.Cure for thalassemia major - from allogeneic hematopoietic stem cell transplantation to gene therapy.Genome editing and stem cell therapy pave the path for new treatment of sickle-cell disease.Transfusion-independent β(0)-thalassemia after bone marrow transplantation failure: proposed involvement of high parental HbF and an epigenetic mechanism.Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies.Management of cardiac hemochromatosis.
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P2860
Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
description
article científic
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article scientifique
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articol științific
@ro
articolo scientifico
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artigo científico
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artigo científico
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artigo científico
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artikel ilmiah
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artikull shkencor
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artículo científico
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name
Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
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type
label
Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
@en
prefLabel
Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
@en
P1476
Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies
@en
P304
P356
10.1182/ASHEDUCATION-2012.1.276
P577
2012-01-01T00:00:00Z