Intraventricular brain injection of adeno-associated virus type 1 (AAV1) in neonatal mice results in complementary patterns of neuronal transduction to AAV2 and total long-term correction of storage lesions in the brains of beta-glucuronidase-defici
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BRI2 (ITM2b) inhibits Abeta deposition in vivoGene therapy for mucopolysaccharidosisEffective gene therapy in an authentic model of Tay-Sachs-related diseasesViral transduction of the neonatal brain delivers controllable genetic mosaicism for visualising and manipulating neuronal circuits in vivo.Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapyRecombinant Adeno-Associated Virus-Mediated microRNA Delivery into the Postnatal Mouse Brain Reveals a Role for miR-134 in Dendritogenesis in VivoRecent advances in the pharmacology of neurological gene therapy.Rapid directional shift of mitochondrial DNA heteroplasmy in animal tissues by a mitochondrially targeted restriction endonucleaseAdeno-associated virus serotypes 1, 8, and 9 share conserved mechanisms for anterograde and retrograde axonal transport.AAV-mediated netrin-1 overexpression increases peri-infarct blood vessel density and improves motor function recovery after experimental strokeGene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease.Intracerebroventricular viral injection of the neonatal mouse brain for persistent and widespread neuronal transduction.Transduction profiles of recombinant adeno-associated virus vectors derived from serotypes 2 and 5 in the nigrostriatal system of rats.CNS-targeted viral delivery of G-CSF in an animal model for ALS: improved efficacy and preservation of the neuromuscular unitExpanded repertoire of AAV vector serotypes mediate unique patterns of transduction in mouse brain.LRRTM3 interacts with APP and BACE1 and has variants associating with late-onset Alzheimer's disease (LOAD).Capsid-expressing DNA in AAV vectors and its elimination by use of an oversize capsid gene for vector production.Capsid serotype and timing of injection determines AAV transduction in the neonatal mice brain.The pathological phenotypes of human TDP-43 transgenic mouse models are independent of downregulation of mouse Tdp-43Improving single injection CSF delivery of AAV9-mediated gene therapy for SMA: a dose-response study in mice and nonhuman primates.Gene therapy for the nervous system: challenges and new strategies.Imaging gene delivery in a mouse model of congenital neuronal ceroid lipofuscinosis.Ex vivo gene therapy using patient iPSC-derived NSCs reverses pathology in the brain of a homologous mouse modelControlling AAV Tropism in the Nervous System with Natural and Engineered Capsids.A review of gene therapy in canine and feline models of lysosomal storage disorders.Transfection of brain capillary endothelial cells in primary culture with defined blood-brain barrier propertiesA Common Phenotype Polymorphism in Mammalian Brains Defined by Concomitant Production of Prolactin and Growth Hormone.Selectively silencing GSK-3 isoforms reduces plaques and tangles in mouse models of Alzheimer's disease.Neural precursor cells and their role in neuro-oncology.Rapid transgene expression in multiple precursor cell types of adult rat subventricular zone mediated by adeno-associated type 1 vectors.Adeno-associated virus vectors: potential applications for cancer gene therapy.RNAi: a potential therapy for the dominantly inherited nucleotide repeat diseases.Merits of combination cortical, subcortical, and cerebellar injections for the treatment of Niemann-Pick disease type AOverexpression of corticotropin-releasing factor in Barrington's nucleus neurons by adeno-associated viral transduction: effects on bladder function and behaviorExpression of Fused in sarcoma mutations in mice recapitulates the neuropathology of FUS proteinopathies and provides insight into disease pathogenesis.Anti-Amyloid-β Single-Chain Antibody Brain Delivery Via AAV Reduces Amyloid Load But May Increase Cerebral Hemorrhages in an Alzheimer's Disease Mouse ModelNeonatal cellular and gene therapies for mucopolysaccharidoses: the earlier the better?Mucopolysaccharidosis IIIB confers enhanced neonatal intracranial transduction by AAV8 but not by 5, 9 or rh10A corticotropin-releasing factor receptor antagonist improves urodynamic dysfunction produced by social stress or partial bladder outlet obstruction in male rats.Fetal Brain-directed AAV Gene Therapy Results in Rapid, Robust, and Persistent Transduction of Mouse Choroid Plexus Epithelia
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P2860
Intraventricular brain injection of adeno-associated virus type 1 (AAV1) in neonatal mice results in complementary patterns of neuronal transduction to AAV2 and total long-term correction of storage lesions in the brains of beta-glucuronidase-defici
description
2003 nî lūn-bûn
@nan
2003年の論文
@ja
2003年学术文章
@wuu
2003年学术文章
@zh-cn
2003年学术文章
@zh-hans
2003年学术文章
@zh-my
2003年学术文章
@zh-sg
2003年學術文章
@yue
2003年學術文章
@zh
2003年學術文章
@zh-hant
name
Intraventricular brain injecti ...... s of beta-glucuronidase-defici
@en
Intraventricular brain injection of adeno-associated virus type 1
@nl
type
label
Intraventricular brain injecti ...... s of beta-glucuronidase-defici
@en
Intraventricular brain injection of adeno-associated virus type 1
@nl
prefLabel
Intraventricular brain injecti ...... s of beta-glucuronidase-defici
@en
Intraventricular brain injection of adeno-associated virus type 1
@nl
P2093
P2860
P1433
P1476
Intraventricular brain injecti ...... s of beta-glucuronidase-defici
@en
P2093
Alyson L Feigenbaum
Charles H Vite
Daniel J Landsburg
Deborah J Watson
John H Wolfe
Marco A Passini
P2860
P304
P356
10.1128/JVI.77.12.7034-7040.2003
P407
P577
2003-06-01T00:00:00Z