Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
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Profile of eliglustat tartrate in the management of Gaucher diseaseA Review of Gaucher Disease Pathophysiology, Clinical Presentation and TreatmentsElevation of glycoprotein nonmetastatic melanoma protein B in type 1 Gaucher disease patients and mouse modelsGlucosylated cholesterol in mammalian cells and tissues: formation and degradation by multiple cellular β-glucosidases.Progress and potential of non-inhibitory small molecule chaperones for the treatment of Gaucher disease and its implications for Parkinson disease.New Directions in Gaucher Disease.Gaucher disease: Progress and ongoing challenges.The Spectrum of Neurological Manifestations Associated with Gaucher Disease.A HILIC-MS/MS method for simultaneous quantification of the lysosomal disease markers galactosylsphingosine and glucosylsphingosine in mouse serum
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P2860
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
description
2015 nî lūn-bûn
@nan
2015年の論文
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2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
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2015年论文
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name
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@en
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@nl
type
label
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@en
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@nl
prefLabel
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@en
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@nl
P2093
P2860
P356
P1433
P1476
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
@en
P2093
Alexander Doyle
André R A Marques
Jan-Eric Månsson
Johannes M Aerts
Karin Olsson
Maria Dahl
Mats Ehinger
Michael Rothe
Mina Mirzaian
Stefan Karlsson
P2860
P304
P356
10.1038/MT.2015.16
P577
2015-02-06T00:00:00Z