Self-complementary AAV vectors; advances and applications.
about
Oligonucleotide therapeutic approaches for Huntington diseaseTherapeutic microRNA delivery suppresses tumorigenesis in a murine liver cancer modelAdeno-associated Virus as a Mammalian DNA VectorCurrent prospects and challenges for epilepsy gene therapyMolecular, genetic and stem cell-mediated therapeutic strategies for spinal muscular atrophy (SMA)AAV-mediated gene therapy in mouse models of recessive retinal degenerationAAV-Delivered Antibody Mediates Significant Protective Effects against SIVmac239 Challenge in the Absence of Neutralizing ActivityNew tools for investigating astrocyte-to-neuron communication.Proof of concept study with an HER-2 mimotope anticancer vaccine deduced from a novel AAV-mimotope library platformLigand-binding domains of nuclear receptors facilitate tight control of split CRISPR activityMassively parallel cis-regulatory analysis in the mammalian central nervous systemPassive immunization against HIV/AIDS by antibody gene transfer.A potassium leak channel silences hyperactive neurons and ameliorates status epilepticusCNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy.Gene delivery to mitochondria by targeting modified adenoassociated virus suppresses Leber's hereditary optic neuropathy in a mouse model.AAV1.NT-3 gene therapy for charcot-marie-tooth neuropathy.Somatic Therapy of a Mouse SMA Model with a U7 snRNA Gene Correcting SMN2 SplicingRedirecting N-acetylaspartate metabolism in the central nervous system normalizes myelination and rescues Canavan disease.Inner limiting membrane barriers to AAV-mediated retinal transduction from the vitreous.High-efficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectorsIntravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons.High-efficiency transient transduction of human embryonic stem cell-derived neurons with baculoviral vectorsGene therapy for monogenic liver diseases: clinical successes, current challenges and future prospects.Gene delivery with viral vectors for cerebrovascular diseases.Transduction of the inner mouse retina using AAVrh8 and AAVrh10 via intravitreal injectionEstablishment of a reverse genetics system for studying human bocavirus in human airway epitheliaAdeno-associated virus: a key to the human genome?Leber's Hereditary Optic Neuropathy-Gene Therapy: From Benchtop to Bedside.Vector platforms for gene therapy of inherited retinopathies.Adeno-associated virus vectors serotype 2 induce prolonged proliferation of capsid-specific CD8+ T cells in mice.Evaluation of lateral spread of transgene expression following subretinal AAV-mediated gene delivery in dogsSafety and effects of the vector for the Leber hereditary optic neuropathy gene therapy clinical trial.Genetic vaccination for re-establishing T-cell tolerance in type 1 diabetes.Efficiency and safety of AAV-mediated gene delivery of the human ND4 complex I subunit in the mouse visual systemVector design influences hepatic genotoxicity after adeno-associated virus gene therapy.The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver.Recombinant AAV-directed gene therapy for type I glycogen storage diseases.Self-complementary AAV2.5-BMP2-coated femoral allografts mediated superior bone healing versus live autografts in mice with equivalent biomechanics to unfractured femur.Distinct transduction profiles in the CNS via three injection routes of AAV9 and the application to generation of a neurodegenerative mouse model.Development of viral vectors for use in cardiovascular gene therapy.
P2860
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P2860
Self-complementary AAV vectors; advances and applications.
description
2008 nî lūn-bûn
@nan
2008 թուականի Օգոստոսին հրատարակուած գիտական յօդուած
@hyw
2008 թվականի օգոստոսին հրատարակված գիտական հոդված
@hy
2008年の論文
@ja
2008年論文
@yue
2008年論文
@zh-hant
2008年論文
@zh-hk
2008年論文
@zh-mo
2008年論文
@zh-tw
2008年论文
@wuu
name
Self-complementary AAV vectors; advances and applications.
@ast
Self-complementary AAV vectors; advances and applications.
@en
Self-complementary AAV vectors; advances and applications.
@nl
type
label
Self-complementary AAV vectors; advances and applications.
@ast
Self-complementary AAV vectors; advances and applications.
@en
Self-complementary AAV vectors; advances and applications.
@nl
prefLabel
Self-complementary AAV vectors; advances and applications.
@ast
Self-complementary AAV vectors; advances and applications.
@en
Self-complementary AAV vectors; advances and applications.
@nl
P356
P1433
P1476
Self-complementary AAV vectors; advances and applications.
@en
P2093
Douglas M McCarty
P304
P356
10.1038/MT.2008.171
P577
2008-08-05T00:00:00Z