Correction of murine hemophilia A following nonmyeloablative transplantation of hematopoietic stem cells engineered to encode an enhanced human factor VIII variant using a safety-augmented retroviral vector.
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Gene therapy for hemophiliaIn vivo efficacy of platelet-delivered, high specific activity factor VIII variantsIn vitro and In vivo Model Systems for Hemophilia A Gene Therapy.Development of Gene Transfer for Induction of Antigen-specific Tolerance.piggyBac-mediated phenotypic correction of factor VIII deficiencyGene therapy for haemophilia: prospects and challenges to prevent or reverse inhibitor formation.Ectopic platelet-delivered factor (F) VIII for the treatment of Hemophilia A: Plasma and platelet FVIII, is it all the same?Delivery of nucleic acid therapeutics by genetically engineered hematopoietic stem cells.Extrahepatic sources of factor VIII potentially contribute to the coagulation cascade correcting the bleeding phenotype of mice with hemophilia A.Platelet-directed gene therapy overcomes inhibitory antibodies to factor VIII.Factor VIII delivered by haematopoietic stem cell-derived B cells corrects the phenotype of haemophilia A mice.
P2860
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P2860
Correction of murine hemophilia A following nonmyeloablative transplantation of hematopoietic stem cells engineered to encode an enhanced human factor VIII variant using a safety-augmented retroviral vector.
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 21 May 2009
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Correction of murine hemophili ...... y-augmented retroviral vector.
@en
Correction of murine hemophili ...... y-augmented retroviral vector.
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type
label
Correction of murine hemophili ...... y-augmented retroviral vector.
@en
Correction of murine hemophili ...... y-augmented retroviral vector.
@nl
prefLabel
Correction of murine hemophili ...... y-augmented retroviral vector.
@en
Correction of murine hemophili ...... y-augmented retroviral vector.
@nl
P2860
P921
P1433
P1476
Correction of murine hemophili ...... y-augmented retroviral vector.
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P2093
Ali Ramezani
Robert G Hawley
P2860
P304
P356
10.1182/BLOOD-2009-01-199653
P407
P577
2009-05-21T00:00:00Z