Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients.
about
Emerging novel concept of chaperone therapies for protein misfolding diseasesDose responsive effects of subcutaneous pentosan polysulfate injection in mucopolysaccharidosis type VI rats and comparison to oral treatmentGene therapy for neurologic manifestations of mucopolysaccharidoses.Safety of laronidase delivered into the spinal canal for treatment of cervical stenosis in mucopolysaccharidosis I.Protease-resistant modified human β-hexosaminidase B ameliorates symptoms in GM2 gangliosidosis modelClinical Improvement of Alpha-mannosidosis Cat Following a Single Cisterna Magna Infusion of AAV1.Pathogenesis and treatment of spine disease in the mucopolysaccharidoses.Intranasal Adeno-Associated Virus Mediated Gene Delivery and Expression of Human Iduronidase in the Central Nervous System: A Noninvasive and Effective Approach for Prevention of Neurologic Disease in Mucopolysaccharidosis Type I.Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model.
P2860
Q27002907-4D3AA26A-EF0A-489B-974F-30C29B97C45BQ27321536-93C5C9E5-117F-4331-9954-0C96883C1093Q35362251-985EB884-B97A-40AA-AE88-8E59E612656CQ36067812-D8C63DCE-0B46-48B4-A2CB-2A01ABB8C8BEQ36867296-36B9BE4D-DD55-4B6F-B55E-8ECD171A53A1Q38471750-BBFE223C-957E-4D3C-8CAB-A36D23887B11Q38853824-0C18CCF3-E380-4ED0-9CAC-A48E07FB30EDQ40219437-4012069C-D831-4922-96BE-1DA6C58596D8Q40663776-B7908243-8981-4CCD-82E4-55C0B4CC7F95
P2860
Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients.
description
article científic
@ca
article scientifique
@fr
articolo scientifico
@it
artigo científico
@pt
bilimsel makale
@tr
scientific article published on 03 September 2013
@en
vedecký článok
@sk
vetenskaplig artikel
@sv
videnskabelig artikel
@da
vědecký článek
@cs
name
Immune response to intrathecal ...... opolysaccharidosis I patients.
@en
Immune response to intrathecal ...... opolysaccharidosis I patients.
@nl
type
label
Immune response to intrathecal ...... opolysaccharidosis I patients.
@en
Immune response to intrathecal ...... opolysaccharidosis I patients.
@nl
prefLabel
Immune response to intrathecal ...... opolysaccharidosis I patients.
@en
Immune response to intrathecal ...... opolysaccharidosis I patients.
@nl
P2093
P2860
P356
P1433
P1476
Immune response to intrathecal ...... opolysaccharidosis I patients.
@en
P2093
Agnes Chen
Anton Mlikotic
David Naylor
Hermes Garban
Ilkka Kaitila
Patricia Dickson
Paul Harmatz
Shih-Hsin Kan
P2860
P2888
P304
P356
10.1038/PR.2013.158
P407
P577
2013-09-03T00:00:00Z