Refining strategies to translate genome editing to the clinic.
about
Traceless Targeting and Isolation of Gene-Edited Immortalized Keratinocytes from Epidermolysis Bullosa Simplex Patients.Targeted genome editing restores T cell differentiation in a humanized X-SCID pluripotent stem cell disease model.TALEN-mediated functional correction of human iPSC-derived macrophages in context of hereditary pulmonary alveolar proteinosis.Immunity to CRISPR Cas9 and Cas12a therapeutics.Efficacy of lentiviral mediated gene therapy in an Omenn syndrome Rag2 mouse model is not hindered by inflammation and immune dysregulation.CRISPR Genome Engineering for Human Pluripotent Stem Cell Research.Structure and Dynamics of Cas9 HNH Domain Catalytic State.Human genetic variation alters CRISPR-Cas9 on- and off-targeting specificity at therapeutically implicated loci.Interferons and beyond: Induction of antiretroviral restriction factors.Stem cells and genome editing: approaches to tissue regeneration and regenerative medicine.The Expanding Therapeutic Perspective of CCR5 Blockade.Updated summary of genome editing technology in human cultured cells linked to human genetics studies.Highly Efficient and Versatile Plasmid-Based Gene Editing in Primary T Cells.Gene Therapy for Chronic HBV-Can We Eliminate cccDNA?The past and presence of gene targeting: from chemicals and DNA via proteins to RNA.Tapping the RNA world for therapeutics.Designer epigenome modifiers enable robust and sustained gene silencing in clinically relevant human cells.Recent Progress in Stem Cell Modification for Cardiac Regeneration.Approaches in Immunotherapy, Regenerative Medicine, and Bioengineering for Type 1 Diabetes.Transient Retrovirus-Based CRISPR/Cas9 All-in-One Particles for Efficient, Targeted Gene KnockoutNeuro-Immuno-Gene- and Genome-Editing-Therapy for Alzheimer's Disease: Are We There Yet?In vivo CRISPR editing with no detectable genome-wide off-target mutationsOrthogonal Cas9-Cas9 chimeras provide a versatile platform for genome editing
P2860
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P2860
Refining strategies to translate genome editing to the clinic.
description
2017 nî lūn-bûn
@nan
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
2017年论文
@zh
2017年论文
@zh-cn
name
Refining strategies to translate genome editing to the clinic.
@en
Refining strategies to translate genome editing to the clinic.
@nl
type
label
Refining strategies to translate genome editing to the clinic.
@en
Refining strategies to translate genome editing to the clinic.
@nl
prefLabel
Refining strategies to translate genome editing to the clinic.
@en
Refining strategies to translate genome editing to the clinic.
@nl
P356
P1433
P1476
Refining strategies to translate genome editing to the clinic.
@en
P2093
Claudio Mussolino
Tatjana I Cornu
P2888
P304
P356
10.1038/NM.4313
P407
P577
2017-04-01T00:00:00Z
P6179
1084537679