A double-blind, placebo-controlled phase II study of the efficacy and safety of 2,2-dimethylbutyrate (HQK-1001), an oral fetal globin inducer, in sickle cell disease.

A double-blind, placebo-controlled phase II study of the efficacy and safety of 2,2-dimethylbutyrate (HQK-1001), an oral fetal globin inducer, in sickle cell disease.

Item
http://www.wikidata.org/entity/Q45377608
Precipitating factors and targeted therapies in combating the perils of sickle cell disease--- A special nutritional considerationBiomarkers and recent advances in the management and therapy of sickle cell disease2015 Clinical trials update in sickle cell anemiaReevaluating the hype: four bacterial metabolites under scrutiny.Pharmacological Induction of Human Fetal Globin Gene in Hydroxyurea-Resistant Primary Adult Erythroid CellsBeyond hydroxyurea: new and old drugs in the pipeline for sickle cell disease.Inactivation of HDAC1 or HDAC2 induces gamma globin expression without altering cell cycle or proliferation.Recent trends in the gene therapy of β-thalassemia.Pediatric sickle cell disease: past successes and future challenges.Peptide nucleic acids targeting β-globin mRNAs selectively inhibit hemoglobin production in murine erythroleukemia cellsTherapeutic advances in sickle cell disease in the last decade.Intrapatient variability in fetal hemoglobin measurements over time in sickle cell patients not on fetal hemoglobin inducing agents.Developing new pharmacotherapeutic approaches to treating sickle-cell disease.Orphan Drugs and Potential Novel Approaches for Therapies of β-Thalassemia: Current Status and Future ExpectationsErythropoiesis: insights into pathophysiology and treatments in 2017.
P2860

A double-blind, placebo-controlled phase II study of the efficacy and safety of 2,2-dimethylbutyrate (HQK-1001), an oral fetal globin inducer, in sickle cell disease.

Item
http://www.wikidata.org/entity/Q45377608
description
2014 nî lūn-bûn
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2014年の論文
@ja
2014年学术文章
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2014年学术文章
@zh
2014年学术文章
@zh-cn
2014年学术文章
@zh-hans
2014年学术文章
@zh-my
2014年学术文章
@zh-sg
2014年學術文章
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2014年學術文章
@zh-hant
name
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@en
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@nl
type
label
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@en
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@nl
prefLabel
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@en
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@nl
P1433
P1476
P2093
P2860
P304
P31
P356
P433
P478
P50
P577
P698
P356
P1433
P1476
A double-blind, placebo-contro ...... ducer, in sickle cell disease.
@en
P2093
P2860
P304
P31
P356
P433
P478
P50
P577
P698