Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis: a multicenter, double-blind, placebo-controlled trial.
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Progress towards gene therapy for cystic fibrosisTopical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung diseaseTopical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung diseaseTopical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung diseaseAdeno-associated virus serotype 2 induces cell-mediated immune responses directed against multiple epitopes of the capsid protein VP1Topical cystic fibrosis transmembrane conductance regulator gene replacement for cystic fibrosis-related lung diseaseNew and emerging targeted therapies for cystic fibrosisAdeno-associated virus for cystic fibrosis gene therapyGene therapy: light is finally in the tunnelAdeno-associated virus: from defective virus to effective vectorHighly compacted biodegradable DNA nanoparticles capable of overcoming the mucus barrier for inhaled lung gene therapyCFTR delivery to 25% of surface epithelial cells restores normal rates of mucus transport to human cystic fibrosis airway epitheliumIntranasal antibody gene transfer in mice and ferrets elicits broad protection against pandemic influenza.Directed evolution of adeno-associated virus yields enhanced gene delivery vectors.AAV's anatomy: roadmap for optimizing vectors for translational successCystic fibrosis: exploiting its genetic basis in the hunt for new therapiesVector serotype screening for use in ovine perinatal lung gene therapy.Attenuation of monocrotaline-induced pulmonary hypertension by luminal adeno-associated virus serotype 9 gene transfer of prostacyclin synthaseNebulisation of receptor-targeted nanocomplexes for gene delivery to the airway epithelium.Characterization of a recombinant adeno-associated virus type 2 Reference Standard MaterialSustained exendin-4 secretion through gene therapy targeting salivary glands in two different rodent models of obesity/type 2 diabetesThe expanding role of aerosols in systemic drug delivery, gene therapy and vaccination: an update.In vivo evaluation of adeno-associated virus gene transfer in airways of mice with acute or chronic respiratory infection.Gene therapy using adeno-associated virus vectorsPrevalence of neutralizing antibodies against adeno-associated virus (AAV) types 2, 5, and 6 in cystic fibrosis and normal populations: Implications for gene therapy using AAV vectors.Species-specific differences in mouse and human airway epithelial biology of recombinant adeno-associated virus transduction.Clinical review: gene-based therapies for ALI/ARDS: where are we now?A 10 patient case report on the impact of plasmapheresis upon neutralizing factors against adeno-associated virus (AAV) types 1, 2, 6, and 8.Viral-mediated gene therapy for the muscular dystrophies: successes, limitations and recent advancesLung inflammation as a therapeutic target in cystic fibrosis.Macromolecular interactions and ion transport in cystic fibrosis.Gene therapy for cystic fibrosis: an example for lung gene therapy.Lentivirus-mediated gene transfer to the respiratory epithelium: a promising approach to gene therapy of cystic fibrosis.Risk of hemoptysis in cystic fibrosis clinical trials: A retrospective cohort studyCell and gene therapy for genetic diseases: inherited disorders affecting the lung and those mimicking sudden infant death syndromeSingle amino acid modification of adeno-associated virus capsid changes transduction and humoral immune profiles.Biological Differences in rAAV Transduction of Airway Epithelia in Humans and in Old World Non-human Primates.Induction of Immune Tolerance to Foreign Protein via Adeno-Associated Viral Vector Gene Transfer in Mid-Gestation Fetal Sheep.Adeno-associated virus-based gene therapy for inherited disorders.Gene transfer in the lung using recombinant adeno-associated virus
P2860
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P2860
Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis: a multicenter, double-blind, placebo-controlled trial.
description
2004 nî lūn-bûn
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2004年の論文
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2004年学术文章
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2004年学术文章
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2004年学术文章
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2004年学术文章
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name
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@en
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@nl
type
label
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@en
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@nl
prefLabel
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@en
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@nl
P2093
P921
P356
P1433
P1476
Repeated adeno-associated viru ...... ind, placebo-controlled trial.
@en
P2093
Alan S Brody
Alison E Heald
Bonnie Ramsey
David Rodman
David Waltz
John P Clancy
L Terry Spencer
Moira L Aitken
Nicole Hamblett
Richard B Moss
P304
P356
10.1378/CHEST.125.2.509
P407
P577
2004-02-01T00:00:00Z