A novel SV40-based vector successfully transduces and expresses an alpha 1-antitrypsin ribozyme in a human hepatoma-derived cell line.
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alpha1-Antitrypsin deficiency . 6: new and emerging treatments for alpha1-antitrypsin deficiencyEvidence for the involvement of Gi2 in activation of extracellular signal-regulated kinases in hepatocytesChallenges and Prospects for Alpha-1 Antitrypsin Deficiency Gene TherapyGene therapy using SV40-derived vectors: what does the future hold?Variables and strategies in development of therapeutic post-transcriptional gene silencing agentsInhibition of hepatitis viral replication by siRNA.Cell and gene therapy for genetic diseases: inherited disorders affecting the lung and those mimicking sudden infant death syndromeGene therapy for alpha-1 antitrypsin deficiency.Recent advances in α-1-antitrypsin deficiency-related lung disease.Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency.Exploiting hepatitis C virus activation of NFkappaB to deliver HCV-responsive expression of interferons alpha and gamma.Sustained miRNA-mediated knockdown of mutant AAT with simultaneous augmentation of wild-type AAT has minimal effect on global liver miRNA profiles.Construction of HBV-specific ribozyme and its recombinant with HDV and their cleavage activity in vitro.Preparation and properties of an alpha-1-protease inhibitor concentrate with high specific activity.HIV-1 proprotein processing as a target for gene therapy.Conditional expression of alpha1-antitrypsin delivered by recombinant SV40 vectors protects lymphocytes against HIV.SV40-derived vectors provide effective transgene expression and inhibition of HIV-1 using constitutive, conditional,and pol III promoters.American Thoracic Society/European Respiratory Society statement: standards for the diagnosis and management of individuals with alpha-1 antitrypsin deficiency.Cre Recombinase Mediates the Removal of Bacterial Backbone to Efficiently Generate rSV40.
P2860
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P2860
A novel SV40-based vector successfully transduces and expresses an alpha 1-antitrypsin ribozyme in a human hepatoma-derived cell line.
description
1999 nî lūn-bûn
@nan
1999年の論文
@ja
1999年論文
@yue
1999年論文
@zh-hant
1999年論文
@zh-hk
1999年論文
@zh-mo
1999年論文
@zh-tw
1999年论文
@wuu
1999年论文
@zh
1999年论文
@zh-cn
name
A novel SV40-based vector succ ...... an hepatoma-derived cell line.
@en
type
label
A novel SV40-based vector succ ...... an hepatoma-derived cell line.
@en
prefLabel
A novel SV40-based vector succ ...... an hepatoma-derived cell line.
@en
P2093
P2860
P356
P1433
P1476
A novel SV40-based vector succ ...... an hepatoma-derived cell line.
@en
P2093
P2860
P2888
P304
P356
10.1038/SJ.GT.3300793
P577
1999-01-01T00:00:00Z
P5875
P6179
1004771026