Gene therapy for the hemoglobin disorders: past, present, and future.
about
Transient in vivo beta-globin production after lentiviral gene transfer to hematopoietic stem cells in the nonhuman primateThe beta-globin locus control region versus gene therapy vectors: a struggle for expression.Genomic editing tools to model human diseases with isogenic pluripotent stem cells.Globin gene transfer for the treatment of severe hemoglobinopathies: a paradigm for stem cell-based gene therapy.Loss of T cell-mediated antitumor immunity after construct-specific downregulation of retrovirally encoded T-cell receptor expression in vivo.Therapeutic challenges in childhood sickle cell disease. Part 1: current and future treatment options.Sustained high-level polyclonal hematopoietic marking and transgene expression 4 years after autologous transplantation of rhesus macaques with SIV lentiviral vector-transduced CD34+ cellsB-cell-specific transgene expression using a self-inactivating retroviral vector with human CD19 promoter and viral post-transcriptional regulatory element.
P2860
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P2860
Gene therapy for the hemoglobin disorders: past, present, and future.
description
2000 nî lūn-bûn
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2000 թուականի Մայիսին հրատարակուած գիտական յօդուած
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2000 թվականի մայիսին հրատարակված գիտական հոդված
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2000年の論文
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2000年論文
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2000年論文
@zh-hant
2000年論文
@zh-hk
2000年論文
@zh-mo
2000年論文
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2000年论文
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name
Gene therapy for the hemoglobin disorders: past, present, and future.
@ast
Gene therapy for the hemoglobin disorders: past, present, and future.
@en
type
label
Gene therapy for the hemoglobin disorders: past, present, and future.
@ast
Gene therapy for the hemoglobin disorders: past, present, and future.
@en
prefLabel
Gene therapy for the hemoglobin disorders: past, present, and future.
@ast
Gene therapy for the hemoglobin disorders: past, present, and future.
@en
P2860
P356
P1476
Gene therapy for the hemoglobin disorders: past, present, and future.
@en
P2093
Nienhuis AW
Persons DA
P2860
P304
P356
10.1073/PNAS.97.10.5022
P407
P577
2000-05-01T00:00:00Z