Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
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The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retinaRestoring the ON Switch in Blind Retinas: Opto-mGluR6, a Next-Generation, Cell-Tailored Optogenetic ToolDosage thresholds for AAV2 and AAV8 photoreceptor gene therapy in monkeyMicroRNA-restricted transgene expression in the retinaAdult human Müller glia cells are a highly efficient source of rod photoreceptorsFunctional and molecular characterization of rod-like cells from retinal stem cells derived from the adult ciliary epitheliumMassively parallel cis-regulatory analysis in the mammalian central nervous systemRestoration of cone vision in the CNGA3-/- mouse model of congenital complete lack of cone photoreceptor functionZinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa.Efficacy of a combined intracerebral and systemic gene delivery approach for the treatment of a severe lysosomal storage disorder.Gene therapy restores vision in rd1 mice after removal of a confounding mutation in Gpr179Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy.Molecular evolution of adeno-associated virus for enhanced glial gene delivery.Optogenetics.Gene therapy with a promoter targeting both rods and cones rescues retinal degeneration caused by AIPL1 mutationsInner limiting membrane barriers to AAV-mediated retinal transduction from the vitreous.High-efficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectorsVascular endothelial growth factor-B gene transfer exacerbates retinal and choroidal neovascularization and vasopermeability without promoting inflammation.Rod Outer Segment Development Influences AAV-Mediated Photoreceptor Transduction After Subretinal Injection.Replacement gene therapy with a human RPGRIP1 sequence slows photoreceptor degeneration in a murine model of Leber congenital amaurosis.A 350 bp region of the proximal promoter of Rds drives cell-type specific gene expression.Reduction of choroidal neovascularization in mice by adeno-associated virus-delivered anti-vascular endothelial growth factor short hairpin RNA.Dendritic spine alterations in neocortical pyramidal neurons following postnatal neuronal Nogo-A knockdown.Successful arrest of photoreceptor and vision loss expands the therapeutic window of retinal gene therapy to later stages of disease.Tropisms of AAV for subretinal delivery to the neonatal mouse retina and its application for in vivo rescue of developmental photoreceptor disorders.Vector platforms for gene therapy of inherited retinopathies.AAV9 targets cone photoreceptors in the nonhuman primate retina.Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retinaTargeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectors.Recombinant adeno-associated virus serotype 6 efficiently transduces primary human melanocytesTargeting channelrhodopsin-2 to ON-bipolar cells with vitreally administered AAV Restores ON and OFF visual responses in blind miceAAV and compacted DNA nanoparticles for the treatment of retinal disorders: challenges and future prospects.AAV-mediated photoreceptor transduction of the pig cone-enriched retina.Long-term and age-dependent restoration of visual function in a mouse model of CNGB3-associated achromatopsia following gene therapyEfficient mutagenesis of the rhodopsin gene in rod photoreceptor neurons in mice.Proof of concept for AAV2/5-mediated gene therapy in iPSC-derived retinal pigment epithelium of a choroideremia patient.Gene Therapy with Endogenous Inhibitors of Angiogenesis for Neovascular Age-Related Macular Degeneration: Beyond Anti-VEGF Therapy.Development of gene therapy for treatment of age-related macular degeneration.Repair of rhodopsin mRNA by spliceosome-mediated RNA trans-splicing: a new approach for autosomal dominant retinitis pigmentosa.Efficient gene delivery to photoreceptors using AAV2/rh10 and rescue of the Rho(-/-) mouse
P2860
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P2860
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
description
2007 nî lūn-bûn
@nan
2007年の論文
@ja
2007年論文
@yue
2007年論文
@zh-hant
2007年論文
@zh-hk
2007年論文
@zh-mo
2007年論文
@zh-tw
2007年论文
@wuu
2007年论文
@zh
2007年论文
@zh-cn
name
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@ast
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@en
type
label
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@ast
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@en
prefLabel
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@ast
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@en
P2093
P2860
P50
P356
P1433
P1476
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
@en
P2093
Carolina Iodice
Claudio Mussolino
Daniela Sanges
Luk H Vandenberghe
Marco Petrillo
Maria Garcia-Hoyos
Mariacarmela Allocca
P2860
P304
11372-11380
P356
10.1128/JVI.01327-07
P407
P577
2007-08-15T00:00:00Z