Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors.
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Huntingtin interacting protein 1 induces apoptosis via a novel caspase-dependent death effector domainDisrupted-in-Schizophrenia-1 (DISC-1): mutant truncation prevents binding to NudE-like (NUDEL) and inhibits neurite outgrowthGene therapy for lipid disordersApolipoprotein A-V gene therapy for disease prevention / treatment:a critical analysisElectron Transport Disturbances and Neurodegeneration: From Albert Szent-Györgyi's Concept (Szeged) till Novel Approaches to Boost Mitochondrial BioenergeticsAdeno-associated virus: from defective virus to effective vectorRecombinant adeno-associated viral (rAAV) vectors mediate efficient gene transduction in cultured neonatal and adult microgliaUltrasound-targeted hepatic delivery of factor IX in hemophiliac mice.Lessons Learned from Animal Models of Inherited Bleeding Disorders.In vivo detection of gene expression in liver by 31P nuclear magnetic resonance spectroscopy employing creatine kinase as a marker gene.Molecular signatures associated with cognitive deficits in schizophrenia: a study of biopsied olfactory neural epithelium.Translational data from adeno-associated virus-mediated gene therapy of hemophilia B in dogsDNA instability in replicating Huntington's disease lymphoblastsTolerance induction to cytoplasmic beta-galactosidase by hepatic AAV gene transfer: implications for antigen presentation and immunotoxicityExon expression in lymphoblastoid cell lines from subjects with schizophrenia before and after glucose deprivation.Apoptosis in ischemic heart diseaseAdeno-associated virus vectors and hematologyGene therapy for the hemophilias.Hepatic gene transfer as a means of tolerance induction to transgene productsImpaired intracellular trafficking of adeno-associated virus type 2 vectors limits efficient transduction of murine fibroblasts.Nonrandom transduction of recombinant adeno-associated virus vectors in mouse hepatocytes in vivo: cell cycling does not influence hepatocyte transduction.Innate immune recognition of viruses and viral vectors.Recruitment of single-stranded recombinant adeno-associated virus vector genomes and intermolecular recombination are responsible for stable transduction of liver in vivo.Correction of factor IX deficiency in mice by embryonic stem cells differentiated in vitro.Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo.Genome-wide expression profiling of human blood reveals biomarkers for Huntington's disease.AAV vectors avoid inflammatory signals necessary to render transduced hepatocyte targets for destructive T cellsPeripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B.Suppression of nonsense mutations in cell culture and mice by multimerized suppressor tRNA genes.Improvements in adenoviral vector technology: overcoming barriers for gene therapy.Gene therapy for the haemophilias.Tauroursodeoxycholic acid, a bile acid, is neuroprotective in a transgenic animal model of Huntington's disease.Haemophilias: advances towards genetic engineering replacement therapy.Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B.Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives.A limited number of transducible hepatocytes restricts a wide-range linear vector dose response in recombinant adeno-associated virus-mediated liver transductionGene therapy for haemophilia: the end of a 'royal pathology' in the third millennium?Cardiac gene therapyThe other, forgotten genome: mitochondrial DNA and mental disorders.Modeling Pulmonary Disease Pathways Using Recombinant Adeno-Associated Virus 6.2.
P2860
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P2860
Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors.
description
1999 nî lūn-bûn
@nan
1999年の論文
@ja
1999年学术文章
@wuu
1999年学术文章
@zh
1999年学术文章
@zh-cn
1999年学术文章
@zh-hans
1999年学术文章
@zh-my
1999年学术文章
@zh-sg
1999年學術文章
@yue
1999年學術文章
@zh-hant
name
Correction of hemophilia B in ...... deno-associated viral vectors.
@en
Correction of hemophilia B in ...... deno-associated viral vectors.
@nl
type
label
Correction of hemophilia B in ...... deno-associated viral vectors.
@en
Correction of hemophilia B in ...... deno-associated viral vectors.
@nl
prefLabel
Correction of hemophilia B in ...... deno-associated viral vectors.
@en
Correction of hemophilia B in ...... deno-associated viral vectors.
@nl
P2093
P2860
P921
P356
P1433
P1476
Correction of hemophilia B in ...... deno-associated viral vectors.
@en
P2093
Bellinger DA
Brinkhous KM
Donahue BA
P2860
P2888
P356
10.1038/13518
P407
P577
1999-01-01T00:00:00Z
P5875
P6179
1034835522