Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia.
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Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirusLong term physiologic modification using rAAV in utero gene-therapyIntramuscular electroporation with the pro-opiomelanocortin gene in rat adjuvant arthritisApolipoprotein A-V gene therapy for disease prevention / treatment:a critical analysisAdeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspectiveGene therapy in an era of emerging treatment options for hemophilia BrAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophyPotential use of T cell receptor genes to modify hematopoietic stem cells for the gene therapy of cancer.Adeno-associated virus vectors and hematologyFull functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy.Kinetics of recombinant adeno-associated virus-mediated gene transfer.Adeno-associated virus vector transduction of vascular smooth muscle cells in vivo.Factor IX ectopically expressed in platelets can be stored in alpha-granules and corrects the phenotype of hemophilia B mice.Evaluation of hydrodynamic limb vein injections in nonhuman primates.Haemophilias: advances towards genetic engineering replacement therapy.Generation of neutralizing activity against human immunodeficiency virus type 1 in serum by antibody gene transfer.Cardiac gene therapyGene therapy for haemophilia.Parvovirus-mediated gene transfer for the haemophilias.AAV hybrid serotypes: improved vectors for gene deliveryPost-Natal knockdown of fukutin-related protein expression in muscle by long-termRNA interference induces dystrophic pathology [corrected]Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins.Therapeutic approaches to muscular dystrophy.Protein replacement therapy and gene transfer in canine models of hemophilia A, hemophilia B, von willebrand disease, and factor VII deficiency.Safety of adeno-associated virus gene therapy vectors: a current evaluation.Long-term regulated expression of growth hormone in mice after intramuscular gene transferCapsid-specific T-cell responses to natural infections with adeno-associated viruses in humans differ from those of nonhuman primatesFactor IX expression in skeletal muscle of a severe hemophilia B patient 10 years after AAV-mediated gene transfer.Gene transfer vector biodistribution: pivotal safety studies in clinical gene therapy development.The persistence of alien genomesAdeno-associated virus vectors: potential applications for cancer gene therapy.Cell targeting in anti-cancer gene therapyCurrent issues in adeno-associated viral vector production.Delivery of recombinant adeno-associated virus-mediated human tissue kallikrein for therapy of chronic renal failure in ratsGene therapy in the treatment of heart failure.Gene therapy for disorders affecting children, progress and potential.Silencing of T lymphocytes by antigen-driven programmed death in recombinant adeno-associated virus vector-mediated gene therapy.Enhanced factor VIII heavy chain for gene therapy of hemophilia AAAV-directed muscular dystrophy gene therapy.Cardiac gene therapy with SERCA2a: from bench to bedside
P2860
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P2860
Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia.
description
1998 nî lūn-bûn
@nan
1998年の論文
@ja
1998年学术文章
@wuu
1998年学术文章
@zh
1998年学术文章
@zh-cn
1998年学术文章
@zh-hans
1998年学术文章
@zh-my
1998年学术文章
@zh-sg
1998年學術文章
@yue
1998年學術文章
@zh-hant
name
Direct intramuscular injection ...... in a dog model of hemophilia.
@en
Direct intramuscular injection ...... in a dog model of hemophilia.
@nl
type
label
Direct intramuscular injection ...... in a dog model of hemophilia.
@en
Direct intramuscular injection ...... in a dog model of hemophilia.
@nl
prefLabel
Direct intramuscular injection ...... in a dog model of hemophilia.
@en
Direct intramuscular injection ...... in a dog model of hemophilia.
@nl
P2093
P356
P1433
P1476
Direct intramuscular injection ...... in a dog model of hemophilia.
@en
P2093
D A Bellinger
J Tazelaar
P E Monahan
R J Samulski
T C Nichols
P2888
P356
10.1038/SJ.GT.3300548
P577
1998-01-01T00:00:00Z
P5875
P6179
1004830922