Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy.
about
Ultramicroscopy as a novel tool to unravel the tropism of AAV gene therapy vectors in the brainGene therapy for metachromatic leukodystrophy.Adeno-associated virus gene therapy with cholesterol 24-hydroxylase reduces the amyloid pathology before or after the onset of amyloid plaques in mouse models of Alzheimer's disease.Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophyTranscription factor induction of human oligodendrocyte progenitor fate and differentiation.Lentivector integration sites in ependymal cells from a model of metachromatic leukodystrophy: non-B DNA as a new factor influencing integration.Gene therapy for lysosomal storage disorders: a good start.Cellular therapy and induced neuronal replacement for Huntington's disease.Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vectorCorrection of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice.Novel candidate disease for gene therapy: metachromatic leukodystrophy.Development of gene therapy for blood disorders: an update.Pharmacokinetics and brain uptake in the rhesus monkey of a fusion protein of arylsulfatase a and a monoclonal antibody against the human insulin receptor.Gene therapy for the neurological manifestations in lysosomal storage disorders.Viral vectors for therapy of neurologic diseases.Enzyme replacement improves ataxic gait and central nervous system histopathology in a mouse model of metachromatic leukodystrophy.Mammalian arylsulfatase A functions as a novel component of the extracellular matrix.Metachromatic leukodystrophy: genetics, pathogenesis and therapeutic options.Sustained induction of neuronal addition to the adult rat neostriatum by AAV4-delivered noggin and BDNF.Neuronal Cholesterol Accumulation Induced by Cyp46a1 Down-Regulation in Mouse Hippocampus Disrupts Brain Lipid HomeostasisCYP46A1 inhibition, brain cholesterol accumulation and neurodegeneration pave the way for Alzheimer's disease.Successful treatment of metachromatic leukodystrophy using bone marrow transplantation of HoxB4 overexpressing cellsComparative efficacy and safety of multiple routes of direct CNS administration of adeno-associated virus gene transfer vector serotype rh.10 expressing the human arylsulfatase A cDNA to nonhuman primates.Long-term correction of biochemical and neurological abnormalities in MLD mice model by neonatal systemic injection of an AAV serotype 9 vector.Partial cure of established disease in an animal model of metachromatic leukodystrophy after intracerebral adeno-associated virus-mediated gene transfer.Muscarinic receptor MR signaling prevents efficient remyelination by human and mouse oligodendrocyte progenitor cells
P2860
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P2860
Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy.
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年学术文章
@wuu
2005年学术文章
@zh-cn
2005年学术文章
@zh-hans
2005年学术文章
@zh-my
2005年学术文章
@zh-sg
2005年學術文章
@yue
2005年學術文章
@zh
2005年學術文章
@zh-hant
name
Intracerebral adeno-associated ...... metachromatic leukodystrophy.
@en
Intracerebral adeno-associated ...... metachromatic leukodystrophy.
@nl
type
label
Intracerebral adeno-associated ...... metachromatic leukodystrophy.
@en
Intracerebral adeno-associated ...... metachromatic leukodystrophy.
@nl
prefLabel
Intracerebral adeno-associated ...... metachromatic leukodystrophy.
@en
Intracerebral adeno-associated ...... metachromatic leukodystrophy.
@nl
P2093
P356
P1476
Intracerebral adeno-associated ...... f metachromatic leukodystrophy
@en
P2093
Abdellatif Benraiss
Caroline Sevin
Debby Van Dam
Delphine Bonnin
Ingrid Laurendeau
Lucie Verot
Marie Vanier
Michel Vidaud
Nathalie Cartier
Patrick Aubourg
P356
10.1093/HMG/DDI425
P50
P577
2005-11-25T00:00:00Z